New cell therapy offers hope for slowing duchenne muscular dystrophy
NCT ID NCT05126758
First seen Jan 07, 2026 · Last updated Apr 25, 2026 · Updated 18 times
Summary
This study tests a cell therapy called deramiocel (CAP-1002) in 106 boys and young men with Duchenne muscular dystrophy (DMD), a genetic disease that weakens muscles over time. Participants receive either deramiocel or a placebo every 3 months for a year, then all can get the real treatment for another year. The goal is to see if deramiocel can slow the loss of arm and heart function.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Akron Children's Hospital
Akron, Ohio, 44308, United States
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Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Arkansas Children's Hospital
Little Rock, Arkansas, 72202, United States
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Children's Health Specialty Care Pavilion
Dallas, Texas, 75207, United States
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital of Los Angeles, Division of Neurology
Los Angeles, California, 90027, United States
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Children's Wisconsin
Milwaukee, Wisconsin, 53226, United States
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Phoenix Children's Hospital
Phoenix, Arizona, 85016, United States
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Rare Disease Research NC LLC
Hillsborough, North Carolina, 27278, United States
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Rare Disease Research, LLC
Atlanta, Georgia, 30329, United States
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Saint Louis Children's Hospital
St Louis, Missouri, 63110, United States
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Seattle Children's
Seattle, Washington, 98105, United States
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UCSD Altman Clinical and Translational Research Institute
La Jolla, California, 92037, United States
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University of California, Davis
Sacramento, California, 95817, United States
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University of Iowa Hospitals and Clinics
Iowa City, Iowa, 52242, United States
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University of Missouri Health Care
Columbia, Missouri, 65212, United States
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University of Utah Hospital
Salt Lake City, Utah, 84112, United States
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University of Virginia Children's Hospital
Charlottesville, Virginia, 22903, United States
Conditions
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