New hope for rare kidney disease: drug trial targets severe cases

NCT ID NCT04580420

First seen Jan 03, 2026 · Last updated May 16, 2026 · Updated 20 times

Summary

This study tests an experimental drug called DCR-PHXC in people with primary hyperoxaluria type 1 (PH1) who have severe kidney damage, whether or not they are on dialysis. The goal is to see if the drug can safely lower oxalate levels in the blood, which may help control the disease. About 28 participants, including children and adults, will take part. Because lifelong treatment is likely needed, this is not a cure but aims to manage the condition.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Clinical Trial Site

    ACTIVE_NOT_RECRUITING

    San Francisco, California, 94143, United States

  • Clinical Trial Site

    ACTIVE_NOT_RECRUITING

    Boston, Massachusetts, 02115, United States

  • Clinical Trial Site

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact

  • Clinical Trial Site

    ACTIVE_NOT_RECRUITING

    New York, New York, 10016, United States

  • Clinical Trial Site

    WITHDRAWN

    Bron, 69677, France

  • Clinical Trial Site

    WITHDRAWN

    Paris, 75019, France

  • Clinical Trial Site

    RECRUITING

    Bonn, 53127, Germany

    Contact

  • Clinical Trial Site

    WITHDRAWN

    Heidelberg, 69120, Germany

  • Clinical Trial Site

    WITHDRAWN

    Roma, 00165, Italy

  • Clinical Trial Site

    RECRUITING

    Beirut, 00001, Lebanon

    Contact

  • Clinical Trial Site

    WITHDRAWN

    Casablanca, 2025, Morocco

  • Clinical Trial Site

    WITHDRAWN

    Oradea, 410469, Romania

  • Clinical Trial Site

    WITHDRAWN

    Oradea, 410562, Romania

  • Clinical Trial Site

    RECRUITING

    Barcelona, 08035, Spain

    Contact

  • Clinical Trial Site

    WITHDRAWN

    Santa Cruz de Tenerife, 38320, Spain

  • Clinical Trial Site

    RECRUITING

    Dubai, +971, United Arab Emirates

    Contact

  • Clinical Trial Site

    WITHDRAWN

    London, NWG 2Q3, United Kingdom

  • Clinical Trial Site

    RECRUITING

    London, WC1N3JH, United Kingdom

    Contact

Conditions

Explore the condition pages connected to this study.