Scientists probe why cystinosis treatment fails to protect the brain

NCT ID NCT02012114

Summary

This study aimed to understand how consistently patients with cystinosis take their cysteamine medication and how that affects cystine levels in their bodies and potential brain complications. Researchers followed 65 patients over two years, using electronic monitors to track pill-taking and brain scans to look for cystine buildup. The goal was to learn if the drug reaches the brain and how treatment adherence influences long-term health.

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Contacts and locations

Locations

  • Hospices Civils de Lyon

    Lyon, 69002, France

Conditions

Explore the condition pages connected to this study.