Cystic fibrosis gene fix shows promise in lab, but study halted

NCT ID NCT05100823

First seen Nov 01, 2025 · Last updated May 14, 2026 · Updated 27 times

Summary

This study aimed to see if a special molecule called an oligonucleotide blocker could repair the genetic instructions in cells from people with cystic fibrosis. Researchers collected cells from 16 patients and tested the molecule in the lab. The study was stopped early, so we don't have final results on whether this approach works in people.

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Contacts and locations

Locations

  • Montpellier University Hospital

    Montpellier, 34090, France

Conditions

Explore the condition pages connected to this study.