Gene therapy CTx1000 enters first human safety trial for ALS

NCT ID NCT07401121

First seen Feb 12, 2026 · Last updated May 17, 2026 · Updated 13 times

Summary

This early-stage study tests a single dose of the gene therapy CTx1000 in 15 people with ALS (Lou Gehrig's disease). The main goal is to see if the treatment is safe and tolerable, not to cure the disease. Participants must have been diagnosed within the last 2 years and be on stable standard medications.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Macquarie University Hospital

    RECRUITING

    Sydney, New South Wales, 2109, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

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