Gene-Editing shot could tame deadly fat levels in kids

NCT ID NCT07371767

First seen Feb 01, 2026 · Last updated May 21, 2026 · Updated 18 times

Summary

This study tests a new treatment called CS-121 for children aged 4 to 18 with a rare condition that causes extremely high levels of fat in the blood (hyperchylomicronemia). The treatment uses gene editing to target a protein that controls fat levels. The main goals are to see if it is safe and if it can lower triglyceride levels. Fifteen children will take part in this early-stage trial.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Shanghai Children's Medical Center

    RECRUITING

    Shanghai, Shanghai Municipality, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.