Scientists search for a way to measure hope in untreatable disease

NCT ID NCT06018519

Summary

This study aims to prepare for future treatment trials for Creatine Transporter Deficiency (CTD), a rare genetic disorder that causes severe intellectual disability, seizures, and movement problems. Researchers will test many different questionnaires, games, and activities on about 200 participants, including patients and healthy volunteers, to find which ones are most suitable for tracking changes in patients with significant cognitive challenges. The goal is to identify reliable tools that can be used to test if future experimental drugs are working.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Woman, mother and child hospital, Hospices Civils de Lyon

    RECRUITING

    Bron, 69500, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.