Lifeline extended: patients get continued access to promising blood disorder drug

NCT ID NCT06173024

Summary

This program allows children and adults with severe Von Willebrand Disease (VWD) to continue receiving an experimental treatment they benefited from in a previous study. It's for patients who have no other good treatment options available in their country and would be harmed if the treatment stopped. The goal is to provide continued access to this medicine until it becomes commercially available or is no longer helpful.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Conditions

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