New study aims to unlock mysteries of rare muscle disorders

NCT ID NCT06630650

First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 28 times

Summary

This study follows 75 people with congenital myasthenic syndromes (CMS) for up to 5 years to see how the disease changes over time. Participants will have regular tests like heart and lung checks, muscle ultrasounds, and MRI scans. The goal is to better understand CMS and improve how we measure its effects, not to test a new treatment.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.