Daily shot could transform life for kids with hemophilia

NCT ID NCT05135559

Summary

This study is testing a new medicine called concizumab to see if it can safely prevent bleeding episodes in children under 12 who have hemophilia A or B. Participants will give themselves a daily injection under the skin for 2 to 4 years. The main goal is to see if this daily treatment reduces the number of bleeds compared to their previous standard treatments.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • 'Ippokrateio' General Hospital of Thessaloniki

    Thessaloniki, 54642, Greece

  • 'Ippokrateio' General Hospital of Thessaloniki

    Thessaloniki, GR 54642, Greece

  • A.O.U policlinico "G. Rodolico-San Marco"

    Catania, 95123, Italy

  • AP-HP-HOPITAL NECKER_Service d'hématologie

    Paris, 75015, France

  • Acibadem Adana Hastanesi

    Adana, 01130, Turkey (Türkiye)

  • Acıbadem Adana Hastanesi-Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • Aghia Sophia Childrens' Hospital

    Athens, GR-11527, Greece

  • Ap-Hp-Hopital de Bicetre-1

    Le Kremlin-Bicêtre, 94275, France

  • Arnold Palmer Children's Hospital

    Orlando, Florida, 32806, United States

  • Augusta Univ/Childrens Hosp-GA

    Augusta, Georgia, 30912, United States

  • Azienda Ospedaliera di Padova

    Padua, 35128, Italy

  • Azienda Ospedaliera-Universitaria Parma

    Parma, 43126, Italy

  • BC Children's Hospital

    Vancouver, British Columbia, V6H 3V4, Canada

  • Birmingham Children's Hospital

    Birmingham, B4 6NH, United Kingdom

  • CHU Constantine BEN BADIS/ Hematology department

    Constantine, 25000, Algeria

  • Centre Hospitalier Metropole Savoie

    Chambéry, 73000, France

  • Centre of Oncology and Hematology, Vilnius University

    Vilnius, LT-08406, Lithuania

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Children's Hosp-New Orleans

    New Orleans, Louisiana, 70118, United States

  • Children's Nebraska

    Omaha, Nebraska, 68114, United States

  • Childrens Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Clinic of Haematology, Fundeni Clinical Institute

    Bucharest, 022328, Romania

  • Cook Children's Hospital-Hematology-Oncology

    Fort Worth, Texas, 76104, United States

  • Dipartimento di Ematologia Univ. Firenze

    Florence, 50134, Italy

  • ECU Sickle Cell Comp Clinic

    Greenville, North Carolina, 27834, United States

  • Ege Universitesi Tip Fakultesi

    Izmir, 35100, Turkey (Türkiye)

  • Ege Üniversitesi Hastanesi- Hematoloji

    Izmir, 35100, Turkey (Türkiye)

  • Evelina London Children's Hospital - Haemophilia

    London, SE1 7EH, United Kingdom

  • Gazi University

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Gazi Üniversitesi Hastanesi- Hematoloji

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Great Ormond Street Hospital for Children

    London, WC1N 3HR, United Kingdom

  • Guwahati Medical College

    Guwahati, Assam, 781032, India

  • Haematology and Blood Bank Department

    Algiers, 16000, Algeria

  • Hospital Nini

    Tripoli, 1434, Lebanon

  • Hospital Pulau Pinang

    George Town, Pulau Pinang, 10450, Malaysia

  • Hospital Regional Universitario de Málaga

    Málaga, 29009, Spain

  • Hospital Sultanah Nur Zahirah

    Kuala Terengganu, Terengganu, 20400, Malaysia

  • Hospital Tunku Azizah

    Kampung Baru, Kuala Lumpur, 50300, Malaysia

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Vall d'Hebron

    Barcelona, 08035, Spain

  • Hospital Virgen de la Arrixaca - Hematología

    El Palmar, Murcia, 30120, Spain

  • Indiana Hemophilia-Thromb Ctr

    Indianapolis, Indiana, 46260, United States

  • J K Lon Hospital

    Jaipur, Rajasthan, 302004, India

  • K.J Somaiya Hospital and Research Centre

    Mumbai, Maharashtra, 400022, India

  • King Chulalongkorn Memorial Hospital_Bangkok_0

    Bangkok, 10330, Thailand

  • King Chulalongkorn Memorial Hospital_Pediatric Hematology-Oncology

    Bangkok, 10330, Thailand

  • Klinisk forskningspost

    Oslo, 0372, Norway

  • Koagulationscentrum

    Gothenburg, 413 46, Sweden

  • MCGM - Comprehensive Thalassemia Care

    Mumbai, Maharashtra, 400066, India

  • McMaster Children's Hospital

    Hamilton, Ontario, L8N 3Z5, Canada

  • Memorial Health University Medical Center

    Savannah, Georgia, 31404, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Nemours Child Orlando Hem/Onc.

    Orlando, Florida, 32827, United States

  • Nirmal Hospital Pvt. Ltd.

    Surat, Gujarat, 395002, India

  • Ochsner Clinic Foundation

    New Orleans, Louisiana, 70121, United States

  • Ondokuz Mayis University Medical Faculty Ped. Haematology

    Samsun, 55139, Turkey (Türkiye)

  • Ondokuz Mayıs Üniversitesi Hastanesi - Hematoloji

    Samsun, 55139, Turkey (Türkiye)

  • PHI University Clinic for Children's Diseases Skopje

    Skopje, 1000, North Macedonia

  • Pediatrics Hematology/Oncology Clinic Battle Building

    Charlottesville, Virginia, 22908, United States

  • Post Graduate Institute of Child Health

    Noida, Uttar Pradesh, 201303, India

  • Rady Childrens Hosp San Diego

    San Diego, California, 92123, United States

  • Ramathibodi Hospital

    Bangkok, 10400, Thailand

  • S.C.B. Medical College

    Cuttack, Odisha, 753007, India

  • SGPGI

    Lucknow, Uttart Pradesh, 226014, India

  • SSSH_Dept. of Clinical Haematology & Haemato Oncology

    Kolhāpur, Maharashtra, 416005, India

  • Sahyadri Super Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Saint George Hospital University Medical Center

    Beirut, 961, Lebanon

  • Saitama Children's Med Centre_Hematology-Oncology

    Saitama, 330-8777, Japan

  • Sarawak General Hospital

    Kuching, Sarawak, 93586, Malaysia

  • Seth GS Medical College & KEM Hospital

    Mumbai, Maharashtra, 400012, India

  • Siriraj Hospital - Hematology and Oncology

    Bangkok, 10700, Thailand

  • Spitalul Clinic Judetean De Urgenta Bihor

    Oradea, 410469, Romania

  • Spitalul Clinic de Urgenta pentru Copii Cluj Napoca

    Cluj-Napoca, 400177, Romania

  • St Christopher Hosp for Child

    Philadelphia, Pennsylvania, 19134, United States

  • St. Marianna University School of Medicine Hospital_Pediatrics

    Kanagawa, 216-8511, Japan

  • Sunpasitthiprasong Hospital_Pediatrics Department

    Ubon Ratchathani, Mueang Distirct,, 34000, Thailand

  • Tallinn Children's Hospital

    Tallinn, 13419, Estonia

  • Texas Children's Hospital_Houston

    Houston, Texas, 77030, United States

  • The Children's Mercy Hospital

    Kansas City, Missouri, 64108, United States

  • UMHAT "Sveta Marina" EAD

    Varna, 9010, Bulgaria

  • UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics

    Plovdiv, 4002, Bulgaria

  • UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology

    Sofia, 1527, Bulgaria

  • University Clinical Center of Republic Srpska (545)

    Banja Luka, 78000, Bosnia and Herzegovina

  • University Clinical Centre Tuzla

    Tuzla, 75000, Bosnia and Herzegovina

  • University Hospitals Bristol & Weston NHS Foundation Trust

    Bristol, BS2 8BJ, United Kingdom

  • University of Colorado Hospital

    Aurora, Colorado, 80045, United States

  • Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa

    Lublin, 20-093, Poland

  • Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego

    Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

  • Uniwersyteckie Centrum Kliniczne

    Gdansk, 80-952, Poland

  • Uniwersyteckie Centrum Kliniczne WUM

    Warsaw, 02-091, Poland

  • Vanderbilt Hemostasis Treatment Clinic

    Nashville, Tennessee, 37212, United States

Conditions

Explore the condition pages connected to this study.