Daily shot could transform life for kids with hemophilia
NCT ID NCT05135559
Summary
This study is testing a new medicine called concizumab to see if it can safely prevent bleeding episodes in children under 12 who have hemophilia A or B. Participants will give themselves a daily injection under the skin for 2 to 4 years. The main goal is to see if this daily treatment reduces the number of bleeds compared to their previous standard treatments.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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'Ippokrateio' General Hospital of Thessaloniki
Thessaloniki, 54642, Greece
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'Ippokrateio' General Hospital of Thessaloniki
Thessaloniki, GR 54642, Greece
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A.O.U policlinico "G. Rodolico-San Marco"
Catania, 95123, Italy
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AP-HP-HOPITAL NECKER_Service d'hématologie
Paris, 75015, France
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Acibadem Adana Hastanesi
Adana, 01130, Turkey (Türkiye)
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Acıbadem Adana Hastanesi-Hematoloji
Adana, 01130, Turkey (Türkiye)
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Aghia Sophia Childrens' Hospital
Athens, GR-11527, Greece
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Ap-Hp-Hopital de Bicetre-1
Le Kremlin-Bicêtre, 94275, France
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Arnold Palmer Children's Hospital
Orlando, Florida, 32806, United States
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Augusta Univ/Childrens Hosp-GA
Augusta, Georgia, 30912, United States
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Azienda Ospedaliera di Padova
Padua, 35128, Italy
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Azienda Ospedaliera-Universitaria Parma
Parma, 43126, Italy
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BC Children's Hospital
Vancouver, British Columbia, V6H 3V4, Canada
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Birmingham Children's Hospital
Birmingham, B4 6NH, United Kingdom
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CHU Constantine BEN BADIS/ Hematology department
Constantine, 25000, Algeria
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Centre Hospitalier Metropole Savoie
Chambéry, 73000, France
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Centre of Oncology and Hematology, Vilnius University
Vilnius, LT-08406, Lithuania
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Charlotte Maxeke Johannesburg Academic Hospital
Parktown, Johannesburg, Gauteng, 2193, South Africa
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Children's Hosp-New Orleans
New Orleans, Louisiana, 70118, United States
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Children's Nebraska
Omaha, Nebraska, 68114, United States
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Childrens Hospital of Chicago
Chicago, Illinois, 60611, United States
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Clinic of Haematology, Fundeni Clinical Institute
Bucharest, 022328, Romania
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Cook Children's Hospital-Hematology-Oncology
Fort Worth, Texas, 76104, United States
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Dipartimento di Ematologia Univ. Firenze
Florence, 50134, Italy
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ECU Sickle Cell Comp Clinic
Greenville, North Carolina, 27834, United States
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Ege Universitesi Tip Fakultesi
Izmir, 35100, Turkey (Türkiye)
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Ege Üniversitesi Hastanesi- Hematoloji
Izmir, 35100, Turkey (Türkiye)
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Evelina London Children's Hospital - Haemophilia
London, SE1 7EH, United Kingdom
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Gazi University
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Gazi Üniversitesi Hastanesi- Hematoloji
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Great Ormond Street Hospital for Children
London, WC1N 3HR, United Kingdom
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Guwahati Medical College
Guwahati, Assam, 781032, India
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Haematology and Blood Bank Department
Algiers, 16000, Algeria
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Hospital Nini
Tripoli, 1434, Lebanon
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Hospital Pulau Pinang
George Town, Pulau Pinang, 10450, Malaysia
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Hospital Regional Universitario de Málaga
Málaga, 29009, Spain
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Hospital Sultanah Nur Zahirah
Kuala Terengganu, Terengganu, 20400, Malaysia
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Hospital Tunku Azizah
Kampung Baru, Kuala Lumpur, 50300, Malaysia
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Vall d'Hebron
Barcelona, 08035, Spain
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Hospital Virgen de la Arrixaca - Hematología
El Palmar, Murcia, 30120, Spain
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Indiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, 46260, United States
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J K Lon Hospital
Jaipur, Rajasthan, 302004, India
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K.J Somaiya Hospital and Research Centre
Mumbai, Maharashtra, 400022, India
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King Chulalongkorn Memorial Hospital_Bangkok_0
Bangkok, 10330, Thailand
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King Chulalongkorn Memorial Hospital_Pediatric Hematology-Oncology
Bangkok, 10330, Thailand
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Klinisk forskningspost
Oslo, 0372, Norway
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Koagulationscentrum
Gothenburg, 413 46, Sweden
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MCGM - Comprehensive Thalassemia Care
Mumbai, Maharashtra, 400066, India
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McMaster Children's Hospital
Hamilton, Ontario, L8N 3Z5, Canada
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Memorial Health University Medical Center
Savannah, Georgia, 31404, United States
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Nemours Child Orlando Hem/Onc.
Orlando, Florida, 32827, United States
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Nirmal Hospital Pvt. Ltd.
Surat, Gujarat, 395002, India
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Ochsner Clinic Foundation
New Orleans, Louisiana, 70121, United States
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Ondokuz Mayis University Medical Faculty Ped. Haematology
Samsun, 55139, Turkey (Türkiye)
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Ondokuz Mayıs Üniversitesi Hastanesi - Hematoloji
Samsun, 55139, Turkey (Türkiye)
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PHI University Clinic for Children's Diseases Skopje
Skopje, 1000, North Macedonia
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Pediatrics Hematology/Oncology Clinic Battle Building
Charlottesville, Virginia, 22908, United States
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Post Graduate Institute of Child Health
Noida, Uttar Pradesh, 201303, India
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Rady Childrens Hosp San Diego
San Diego, California, 92123, United States
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Ramathibodi Hospital
Bangkok, 10400, Thailand
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S.C.B. Medical College
Cuttack, Odisha, 753007, India
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SGPGI
Lucknow, Uttart Pradesh, 226014, India
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SSSH_Dept. of Clinical Haematology & Haemato Oncology
Kolhāpur, Maharashtra, 416005, India
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Sahyadri Super Speciality Hospital
Pune, Maharashtra, 411004, India
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Saint George Hospital University Medical Center
Beirut, 961, Lebanon
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Saitama Children's Med Centre_Hematology-Oncology
Saitama, 330-8777, Japan
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Sarawak General Hospital
Kuching, Sarawak, 93586, Malaysia
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Seth GS Medical College & KEM Hospital
Mumbai, Maharashtra, 400012, India
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Siriraj Hospital - Hematology and Oncology
Bangkok, 10700, Thailand
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Spitalul Clinic Judetean De Urgenta Bihor
Oradea, 410469, Romania
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Spitalul Clinic de Urgenta pentru Copii Cluj Napoca
Cluj-Napoca, 400177, Romania
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St Christopher Hosp for Child
Philadelphia, Pennsylvania, 19134, United States
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St. Marianna University School of Medicine Hospital_Pediatrics
Kanagawa, 216-8511, Japan
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Sunpasitthiprasong Hospital_Pediatrics Department
Ubon Ratchathani, Mueang Distirct,, 34000, Thailand
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Tallinn Children's Hospital
Tallinn, 13419, Estonia
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Texas Children's Hospital_Houston
Houston, Texas, 77030, United States
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The Children's Mercy Hospital
Kansas City, Missouri, 64108, United States
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UMHAT "Sveta Marina" EAD
Varna, 9010, Bulgaria
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UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics
Plovdiv, 4002, Bulgaria
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UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology
Sofia, 1527, Bulgaria
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University Clinical Center of Republic Srpska (545)
Banja Luka, 78000, Bosnia and Herzegovina
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University Clinical Centre Tuzla
Tuzla, 75000, Bosnia and Herzegovina
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University Hospitals Bristol & Weston NHS Foundation Trust
Bristol, BS2 8BJ, United Kingdom
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University of Colorado Hospital
Aurora, Colorado, 80045, United States
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Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa
Lublin, 20-093, Poland
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Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego
Wroclaw, Lower Silesian Voivodeship, 50-556, Poland
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Uniwersyteckie Centrum Kliniczne
Gdansk, 80-952, Poland
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Uniwersyteckie Centrum Kliniczne WUM
Warsaw, 02-091, Poland
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Vanderbilt Hemostasis Treatment Clinic
Nashville, Tennessee, 37212, United States
Conditions
Explore the condition pages connected to this study.