Daily shot aims to stop dangerous bleeds in complex haemophilia
NCT ID NCT04083781
Summary
This study is testing a new medicine called concizumab to see if it can safely prevent bleeding episodes in people with haemophilia A or B who have developed inhibitors. Participants will give themselves a daily injection under the skin at home for up to seven years. The goal is to provide a new long-term treatment option to control this serious bleeding disorder.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Acıbadem Adana Hastanesi-Hematoloji
Adana, 01130, Turkey (Türkiye)
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Akdeniz Üniversitesi Hastanesi- Hematoloji
Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)
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All India Institute of Medical Sciences_New Dehli
New Dehli, New Delhi, 110029, India
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All India Institute of Medical Sciences_New Dehli
New Delhi, 110029, India
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Ap-Hp-Hopital de Bicetre
Le Kremlin-Bicêtre, 94270, France
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Azienda OU "S.Maria della Misericordia"
Udine, 33100, Italy
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Azienda Ospedaliera Universitaria Integrata Verona - Ospedale Donna Bambino Borgo Trento - U.O.C. Oncoematologia Pediatrica
Verona, 37126, Italy
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CHU Constantine BEN BADIS/ Hematology department
Constantine, 25000, Algeria
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CMCV
Ranipet, Tamil Nadu, 632 517, India
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CMCV
Ranipet, Tamil Nadu, 632517, India
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Center for Inherited Blood Dis
Orange, California, 92868, United States
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Centre Hospitalier Universitaire de Rennes - Hopital Pontchaillou
Rennes, 35000, France
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Centre Hospitalier de Clermont-Ferrand-Hopital Estaing
Clermont-Ferrand, 63100, France
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Charlotte Maxeke Johannesburg Academic Hospital
Parktown, Johannesburg, Gauteng, 2193, South Africa
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Children Regional Clinical Hospital
Krasnodar, 350007, Russia
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Children's Healthcare Atlanta
Atlanta, Georgia, 30329, United States
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City out-patient clinic 37, City Hemophilia Centre
Saint Petersburg, 191186, Russia
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Clinical Centre of Serbia, Institute for Haematology
Belgrade, 11000, Serbia
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Clinical Centre of Vojvodina
Novi Sad, 21000, Serbia
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Daejeon Eulji Medical Center, Eulji University
Daejeon, 35233, South Korea
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Dipartimento di Ematologia Univ. Firenze
Florence, FI, 50134, Italy
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Fakultni Nemocnice Motol A Homolka
Prague, 150 18, Czechia
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Fiona Stanley Hospital - Haemophilia and Haemostasis Centre
Murdoch, Western Australia, 6150, Australia
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Great Ormond Street Hospital for Children
London, WC1N 3HR, United Kingdom
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Haematology Clinic
Durban, KwaZulu-Natal, 4013, South Africa
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Haematology and Blood Bank Department
Algiers, 16000, Algeria
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Hamltn Hth Sci/McMstr Child Hosp
Hamilton, Ontario, L8N 3Z5, Canada
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Hospices Civils de Lyon- Hopital Louis Pradel
Bron, 69500, France
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Central de Asturias
Oviedo, 33011, Spain
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Hospital Pulau Pinang_Georgetown, Penang
George Town, Pulau Pinang, 10450, Malaysia
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Hospital Queen Elizabeth 1
Kota Kinabalu, Sabah, 88586, Malaysia
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Hospital Regional Universitario de Málaga
Málaga, 29010, Spain
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Hospital Univ. Central de Asturias
Oviedo, 33011, Spain
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Hospital Universitario Dr. José Eleuterio González
Monterrey, Nuevo León, 64460, Mexico
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Universitario Regional de Málaga
Málaga, 29010, Spain
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Hospital Vall d'Hebron
Barcelona, 08035, Spain
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Hospital Virgen del Rocío
Seville, 41013, Spain
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Indiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, 46260, United States
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Institute for Health Care of Children and Adolescents
Novi Sad, 21000, Serbia
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Institute for Mother and Child Health Care of Serbia
Belgrade, 11070, Serbia
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Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery
Lviv, 79044, Ukraine
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Instytut Hematologii i Transfuzjologii
Warsaw, Masovian Voivodeship, 02-776, Poland
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Istituto Oncologico Veneto - Oncoematologia IOV
Castelfranco Veneto, 31033, Italy
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Istituto di Medicina Int. A. Bianchi Bonomi Univ. Milano
Milan, 20124, Italy
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KBC Zagreb, Rebro, Hemofilija centar
Zagreb, 10 000, Croatia
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KBC Zagreb, Zavod za pedijatrijsku hematologiju
Zagreb, 10000, Croatia
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KBC Zagreb_Hematology
Zagreb, 10 000, Croatia
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Kagoshima City Hospital
Kagoshima, 890-8760, Japan
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Kagoshima City Hospital_Pediatrics
Kagoshima, 890-8760, Japan
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Klin. Abt. f. Hämatologie und Hämostaseologie, AKH Wien
Vienna, 1090, Austria
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Koagulationsmottagning - SUS
Malmo, 214 28, Sweden
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Koagulationsmottagningen - KS
Solna, 171 64, Sweden
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Maharaj Nakorn Chiang Mai Hospital _Pediatric Hematology and Oncology
Chiang Mai, 50200, Thailand
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Manchester Royal Infirmary_Manchester
Manchester, M13 9WL, United Kingdom
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Mie University Hospital_Dept.of Blood Trans.Med & Cell
Mie, 514-8507, Japan
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Morozovskaya municipal children hospital
Moscow, 119049, Russia
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Nagoya University Hospital_Blood Transfusion
Aichi, 466-8560, Japan
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Nara Medical University Hospital_Pediatrics
Nara, 634-8522, Japan
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National Medical Research institution of haemotology
Moscow, 125167, Russia
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National specialized children's hospital 'OHMATDYT' - Haemostasis centre
Kyiv, 01135, Ukraine
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Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz
Bratislava, 851 07, Slovakia
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Ogikubo Hospital_Pediatries & Blood
Tokyo, 167-0035, Japan
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Oncoematologia IOV
Castelfranco Veneto, 31033, Italy
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Ospedale Donna Bambino U.O.C. Oncoematologia Pediatrica
Verona, 37126, Italy
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Pietersburg Hospital
Polokwane, Limpopo, 0699, South Africa
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Queen Elizabeth Hospital, Birmingham - Haemophilia
Birmingham, B15 2TH, United Kingdom
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Queen's Medical Centre - Haemophilia Comprehensive Care Centre
Nottingham, NG7 2UH, United Kingdom
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Ramathibodi Hospital_Department of Haematology
Bangkok, 10400, Thailand
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Republican Hospital n.a. V. A. Baranov
Petrozavodsk, 185019, Russia
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Rikshospitalet - avdeling for blodsykdommer
Oslo, 0027, Norway
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Royal Hallamshire Hospital
Sheffield, S10 2JF, United Kingdom
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SPSK nr 1 Klinika Hematoonkologii i Transplantacji Szpiku
Lublin, 20-081, Poland
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Sahyadri Speciality Hospital
Pune, Maharashtra, 411004, India
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Sahyadri Super Speciality Hospital
Pune, Maharashtra, 411004, India
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Saitama Medical Univ. Hospital_Dep of Int Med, Cent for Hemo
Saitama, 350-0495, Japan
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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Skejby Blodsygdomme, blødercentret
Aarhus N, 8200, Denmark
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St. John's Medical college and Hospital
Bangalore, Karnataka, 560034, India
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St. Jude Affiliate Clinic at Novant Health Hemby Children's
Charlotte, North Carolina, 28204, United States
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St. Marianna University School of Medicine Hospital_Pediatrics
Kanagawa, 216-8511, Japan
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Sunpasitthiprasong Hospital_Pediatrics Department
Ubon Ratchathani, Mueang Distirct,, 34000, Thailand
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Szpital Uniwersytecki, Oddzial Kliniczny Hematologii
Krakow, Lesser Poland Voivodeship, 30-688, Poland
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The Alfred
Melbourne, Victoria, 3004, Australia
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The Royal Children's Hospital
Parkville, Victoria, 3052, Australia
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TriStar Medical Group Children's Specialist
Nashville, Tennessee, 37203, United States
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ULS São João, E.P.E.
Porto, 4200-319, Portugal
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UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology
Sofia, 1527, Bulgaria
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University Clinical Centre Kragujevac
Kragujevac, 34000, Serbia
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University of Texas San Antonio
San Antonio, Texas, 78229, United States
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Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Wroclaw, 50-367, Poland
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Uniwersytecki Szpital Kliniczny W Poznaniu
Poznan, Greater Poland Voivodeship, 60-569, Poland
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Uniwersytecki Szpital Kliniczny nr 1 Klinika Hematoonkologii i Transplantacji Szpiku
Lublin, 20-081, Poland
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Ustav Hematologie a krevni tranfuze
Prague, 12000, Czechia
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Washington University School of Medicine_St. Louis
St Louis, Missouri, 63110, United States
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Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi- Hematoloji
Adana, 01130, Turkey (Türkiye)
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İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
Conditions
Explore the condition pages connected to this study.