Daily shot aims to stop dangerous bleeds in complex haemophilia

NCT ID NCT04083781

Summary

This study is testing a new medicine called concizumab to see if it can safely prevent bleeding episodes in people with haemophilia A or B who have developed inhibitors. Participants will give themselves a daily injection under the skin at home for up to seven years. The goal is to provide a new long-term treatment option to control this serious bleeding disorder.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for HAEMOPHILIA A WITH INHIBITORS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Acıbadem Adana Hastanesi-Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • Akdeniz Üniversitesi Hastanesi- Hematoloji

    Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)

  • All India Institute of Medical Sciences_New Dehli

    New Dehli, New Delhi, 110029, India

  • All India Institute of Medical Sciences_New Dehli

    New Delhi, 110029, India

  • Ap-Hp-Hopital de Bicetre

    Le Kremlin-Bicêtre, 94270, France

  • Azienda OU "S.Maria della Misericordia"

    Udine, 33100, Italy

  • Azienda Ospedaliera Universitaria Integrata Verona - Ospedale Donna Bambino Borgo Trento - U.O.C. Oncoematologia Pediatrica

    Verona, 37126, Italy

  • CHU Constantine BEN BADIS/ Hematology department

    Constantine, 25000, Algeria

  • CMCV

    Ranipet, Tamil Nadu, 632 517, India

  • CMCV

    Ranipet, Tamil Nadu, 632517, India

  • Center for Inherited Blood Dis

    Orange, California, 92868, United States

  • Centre Hospitalier Universitaire de Rennes - Hopital Pontchaillou

    Rennes, 35000, France

  • Centre Hospitalier de Clermont-Ferrand-Hopital Estaing

    Clermont-Ferrand, 63100, France

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Children Regional Clinical Hospital

    Krasnodar, 350007, Russia

  • Children's Healthcare Atlanta

    Atlanta, Georgia, 30329, United States

  • City out-patient clinic 37, City Hemophilia Centre

    Saint Petersburg, 191186, Russia

  • Clinical Centre of Serbia, Institute for Haematology

    Belgrade, 11000, Serbia

  • Clinical Centre of Vojvodina

    Novi Sad, 21000, Serbia

  • Daejeon Eulji Medical Center, Eulji University

    Daejeon, 35233, South Korea

  • Dipartimento di Ematologia Univ. Firenze

    Florence, FI, 50134, Italy

  • Fakultni Nemocnice Motol A Homolka

    Prague, 150 18, Czechia

  • Fiona Stanley Hospital - Haemophilia and Haemostasis Centre

    Murdoch, Western Australia, 6150, Australia

  • Great Ormond Street Hospital for Children

    London, WC1N 3HR, United Kingdom

  • Haematology Clinic

    Durban, KwaZulu-Natal, 4013, South Africa

  • Haematology and Blood Bank Department

    Algiers, 16000, Algeria

  • Hamltn Hth Sci/McMstr Child Hosp

    Hamilton, Ontario, L8N 3Z5, Canada

  • Hospices Civils de Lyon- Hopital Louis Pradel

    Bron, 69500, France

  • Hospital Ampang

    Ampang, Selangor, 68000, Malaysia

  • Hospital Ampang

    Ampang, Selangor, 68000, Malaysia

  • Hospital Central de Asturias

    Oviedo, 33011, Spain

  • Hospital Pulau Pinang_Georgetown, Penang

    George Town, Pulau Pinang, 10450, Malaysia

  • Hospital Queen Elizabeth 1

    Kota Kinabalu, Sabah, 88586, Malaysia

  • Hospital Regional Universitario de Málaga

    Málaga, 29010, Spain

  • Hospital Univ. Central de Asturias

    Oviedo, 33011, Spain

  • Hospital Universitario Dr. José Eleuterio González

    Monterrey, Nuevo León, 64460, Mexico

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Universitario Regional de Málaga

    Málaga, 29010, Spain

  • Hospital Vall d'Hebron

    Barcelona, 08035, Spain

  • Hospital Virgen del Rocío

    Seville, 41013, Spain

  • Indiana Hemophilia-Thromb Ctr

    Indianapolis, Indiana, 46260, United States

  • Institute for Health Care of Children and Adolescents

    Novi Sad, 21000, Serbia

  • Institute for Mother and Child Health Care of Serbia

    Belgrade, 11070, Serbia

  • Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery

    Lviv, 79044, Ukraine

  • Instytut Hematologii i Transfuzjologii

    Warsaw, Masovian Voivodeship, 02-776, Poland

  • Istituto Oncologico Veneto - Oncoematologia IOV

    Castelfranco Veneto, 31033, Italy

  • Istituto di Medicina Int. A. Bianchi Bonomi Univ. Milano

    Milan, 20124, Italy

  • KBC Zagreb, Rebro, Hemofilija centar

    Zagreb, 10 000, Croatia

  • KBC Zagreb, Zavod za pedijatrijsku hematologiju

    Zagreb, 10000, Croatia

  • KBC Zagreb_Hematology

    Zagreb, 10 000, Croatia

  • Kagoshima City Hospital

    Kagoshima, 890-8760, Japan

  • Kagoshima City Hospital_Pediatrics

    Kagoshima, 890-8760, Japan

  • Klin. Abt. f. Hämatologie und Hämostaseologie, AKH Wien

    Vienna, 1090, Austria

  • Koagulationsmottagning - SUS

    Malmo, 214 28, Sweden

  • Koagulationsmottagningen - KS

    Solna, 171 64, Sweden

  • Maharaj Nakorn Chiang Mai Hospital _Pediatric Hematology and Oncology

    Chiang Mai, 50200, Thailand

  • Manchester Royal Infirmary_Manchester

    Manchester, M13 9WL, United Kingdom

  • Mie University Hospital_Dept.of Blood Trans.Med & Cell

    Mie, 514-8507, Japan

  • Morozovskaya municipal children hospital

    Moscow, 119049, Russia

  • Nagoya University Hospital_Blood Transfusion

    Aichi, 466-8560, Japan

  • Nara Medical University Hospital_Pediatrics

    Nara, 634-8522, Japan

  • National Medical Research institution of haemotology

    Moscow, 125167, Russia

  • National specialized children's hospital 'OHMATDYT' - Haemostasis centre

    Kyiv, 01135, Ukraine

  • Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz

    Bratislava, 851 07, Slovakia

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Oncoematologia IOV

    Castelfranco Veneto, 31033, Italy

  • Ospedale Donna Bambino U.O.C. Oncoematologia Pediatrica

    Verona, 37126, Italy

  • Pietersburg Hospital

    Polokwane, Limpopo, 0699, South Africa

  • Queen Elizabeth Hospital, Birmingham - Haemophilia

    Birmingham, B15 2TH, United Kingdom

  • Queen's Medical Centre - Haemophilia Comprehensive Care Centre

    Nottingham, NG7 2UH, United Kingdom

  • Ramathibodi Hospital_Department of Haematology

    Bangkok, 10400, Thailand

  • Republican Hospital n.a. V. A. Baranov

    Petrozavodsk, 185019, Russia

  • Rikshospitalet - avdeling for blodsykdommer

    Oslo, 0027, Norway

  • Royal Hallamshire Hospital

    Sheffield, S10 2JF, United Kingdom

  • SPSK nr 1 Klinika Hematoonkologii i Transplantacji Szpiku

    Lublin, 20-081, Poland

  • Sahyadri Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Sahyadri Super Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Saitama Medical Univ. Hospital_Dep of Int Med, Cent for Hemo

    Saitama, 350-0495, Japan

  • Severance Hospital, Yonsei University Health System

    Seoul, 03722, South Korea

  • Skejby Blodsygdomme, blødercentret

    Aarhus N, 8200, Denmark

  • St. John's Medical college and Hospital

    Bangalore, Karnataka, 560034, India

  • St. Jude Affiliate Clinic at Novant Health Hemby Children's

    Charlotte, North Carolina, 28204, United States

  • St. Marianna University School of Medicine Hospital_Pediatrics

    Kanagawa, 216-8511, Japan

  • Sunpasitthiprasong Hospital_Pediatrics Department

    Ubon Ratchathani, Mueang Distirct,, 34000, Thailand

  • Szpital Uniwersytecki, Oddzial Kliniczny Hematologii

    Krakow, Lesser Poland Voivodeship, 30-688, Poland

  • The Alfred

    Melbourne, Victoria, 3004, Australia

  • The Royal Children's Hospital

    Parkville, Victoria, 3052, Australia

  • TriStar Medical Group Children's Specialist

    Nashville, Tennessee, 37203, United States

  • ULS São João, E.P.E.

    Porto, 4200-319, Portugal

  • UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology

    Sofia, 1527, Bulgaria

  • University Clinical Centre Kragujevac

    Kragujevac, 34000, Serbia

  • University of Texas San Antonio

    San Antonio, Texas, 78229, United States

  • Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu

    Wroclaw, 50-367, Poland

  • Uniwersytecki Szpital Kliniczny W Poznaniu

    Poznan, Greater Poland Voivodeship, 60-569, Poland

  • Uniwersytecki Szpital Kliniczny nr 1 Klinika Hematoonkologii i Transplantacji Szpiku

    Lublin, 20-081, Poland

  • Ustav Hematologie a krevni tranfuze

    Prague, 12000, Czechia

  • Washington University School of Medicine_St. Louis

    St Louis, Missouri, 63110, United States

  • Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi- Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.