Daily shot could transform life for people with haemophilia
NCT ID NCT04082429
Summary
This study is testing whether a new medicine called concizumab can safely prevent bleeding episodes in people with haemophilia A or B who do not have inhibitors. Participants will give themselves a daily injection at home and track their bleeds. The goal is to see if this daily treatment works better than only treating bleeds as they happen.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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A.O.U Città Salute Scienza Torino
Torino, 10126, Italy
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Acıbadem Adana Hastanesi-Hematoloji
Adana, 01130, Turkey (Türkiye)
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Belfast City Hospital
Belfast, BT9 7AB, United Kingdom
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CHU Constantine BEN BADIS/ Hematology department
Constantine, 25000, Algeria
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CHU de Caen - Côte de Nacre
Caen, 14033, France
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CMCV
Ranipet, Tamil Nadu, 632517, India
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Center for Blood Disorders Augusta University
Augusta, Georgia, 30912, United States
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Center for Inherited Blood Disorders
Orange, California, 92868, United States
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Centre Hospitalier Regional Et Universitaire de Brest-Hopital de La Cavale Blanche
Brest, 29200, France
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Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu
Nantes, 44093, France
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Centre Hospitalier Universitaire de Saint Etienne-Hopital Nord
Saint-Priest-en-Jarez, 42270, France
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Charlotte Maxeke Johannesburg Academic Hospital
Parktown, Johannesburg, Gauteng, 2193, South Africa
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Children Oncohaematology department Children's Hospital,
Vilnius, 08406, Lithuania
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Children Regional Clinical Hospital
Krasnodar, 350007, Russia
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Children's Hospital Los Angeles - Endocrinology
Los Angeles, California, 90027, United States
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Children's Hospital of Michigan
Detroit, Michigan, 48201, United States
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City out-patient clinic 37, City Hemophilia Centre
Saint Petersburg, 191186, Russia
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Clinical Centre of Serbia, Institute for Haematology
Belgrade, 11000, Serbia
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Clinical Centre of Vojvodina
Novi Sad, 21000, Serbia
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Copenhagen Center for Heamatology
Copenhagen, 2100, Denmark
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Daejeon Eulji Medical Center, Eulji University
Daejeon, 35233, South Korea
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Daejeon Eulji University Hospital
Daejeon, 35233, South Korea
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Dipartimento di Ematologia Univ. Firenze
Florence, FI, 50134, Italy
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Eastern Health Authority
St. John's, Newfoundland and Labrador, A1B 3V6, Canada
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Ege Üniversitesi Hastanesi- Hematoloji
Izmir, 35100, Turkey (Türkiye)
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Fiona Stanley Hospital - Haemophilia and Haemostasis Centre
Murdoch, Western Australia, 6150, Australia
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Gazi University
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Gazi Üniversitesi Hastanesi- Hematoloji
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Hacettepe University Medical Faculty
Ankara, 06230, Turkey (Türkiye)
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Hacettepe Üniversitesi Hastanesi- Endokrinoloji
Ankara, 06230, Turkey (Türkiye)
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Haematology and Blood Bank Department
Algiers, 16000, Algeria
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Hamltn Hth Sci/McMstr Child Hosp
Hamilton, Ontario, L8N 3Z5, Canada
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Hiroshima University Hospital, Hematology
Hiroshima, 734-8551, Japan
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Hiroshima University Hospital_Hematology
Hiroshima, 734-8551, Japan
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Hopital de Bicetre
Le Kremlin-Bicêtre, 94270, France
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Regional Universitario de Málaga
Málaga, 29010, Spain
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Hospital Univ. Central de Asturias
Oviedo, 33011, Spain
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Hospital Universitario Dr. José Eleuterio González
Monterrey, Nuevo León, 64460, Mexico
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Universitario y Politécnico La Fe
Valencia, 46026, Spain
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Hospital Virgen del Rocío
Seville, 41013, Spain
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Hyogo prefectural kobe children's hospital
Hyōgo, 654-0047, Japan
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Hyogo prefectural kobe children's hospital Dept. of Haem and Onclogy
Hyōgo, 654-0047, Japan
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Hôpital Pontchaillou
Rennes, 35033, France
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Indiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, 46260, United States
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Institute for Mother and Child Health Care of Serbia
Belgrade, 11070, Serbia
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Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery
Lviv, 79044, Ukraine
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Instytut Hematologii i Transfuzjologii
Warsaw, Masovian Voivodeship, 02-776, Poland
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Istituto di Medicina Int. A. Bianchi Bonomi Univ. Milano
Milan, MI, 20124, Italy
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Itoigawa sogo Hospital_Department of Pediatrics
Niigata, 941-8502, Japan
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J K Lon Hospital
Jaipur, Rajasthan, 302004, India
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Jeju National University Hospital
Jeju City, 63241, South Korea
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Jeju National University Hospital
Jeju-do, 63241, South Korea
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KBC Zagreb_Hematology
Zagreb, 10 000, Croatia
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Koagulationsmottagning - SUS
Malmo, 214 28, Sweden
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Koagulationsmottagningen
Solna, 171 64, Sweden
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M.S. Hershey Medical Center
Hershey, Pennsylvania, 17033, United States
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MH Eü. Központ -Orszagos Haemophilia Kozpont
Budapest, H-1134, Hungary
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Michigan State University
Lansing, Michigan, 48911, United States
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Morozovskaya municipal children hospital
Moscow, 119049, Russia
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Nagoya University Hospital_Blood Transfusion
Aichi, 466-8560, Japan
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National Center for Child Health and Development_Hematology
Tokyo, 157-8535, Japan
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National Medical Research institution of haemotology
Moscow, 125167, Russia
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National specialized children's hospital 'OHMATDYT' - Haemostasis centre
Kyiv, 01135, Ukraine
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Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz
Bratislava, 851 07, Slovakia
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North Estonia Medical Centre Foundation
Tallinn, 13419, Estonia
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Novant Hlth Vasc Ins Charlotte
Charlotte, North Carolina, 28204, United States
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Ogikubo Hospital_Pediatries & Blood
Tokyo, 167-0035, Japan
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Ondokuz Mayıs Üniversitesi Hastanesi - Hematoloji
Samsun, 55139, Turkey (Türkiye)
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Osaka National Hospital_Dept. of Infectious diseases
Osaka, 546-0006, Japan
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Pietersburg Hospital
Polokwane, Limpopo, 0699, South Africa
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Policlinico Umberto I Sezione Ematologia
Roma, 00161, Italy
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Ramathibodi Hospital_Department of Haematology
Bangkok, 10400, Thailand
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Republican Hospital n.a. V. A. Baranov
Petrozavodsk, 185019, Russia
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Royal Children's Hospital
Parkville, Victoria, 3052, Australia
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Royal Free Haemophilia Comprehensive Care Center
London, NW3 2QG, United Kingdom
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Royal Free Hospital - Haemophilia
London, NW3 2QG, United Kingdom
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Royal Hallamshire Hospital
Sheffield, S10 2JF, United Kingdom
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Sahyadri Speciality Hospital
Pune, Maharashtra, 411004, India
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Sahyadri Super Speciality Hospital
Pune, Maharashtra, 411004, India
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Saitama Children's Med Centre_Hematology-Oncology
Saitama, 330-8777, Japan
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Saitama Medical Univ. Hospital
Saitama, 350-0495, Japan
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Saitama Medical Univ. Hospital_Dep of Int Med, Cent for Hemo
Saitama, 350-0495, Japan
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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Sheba MC The Israeli National Hemophilia Center
Tel Litwinsky, 52621, Israel
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Shizuoka Children's Hospital
Shizuoka, 420-8660, Japan
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Shizuoka Children's Hospital, Hematology-Oncology
Shizuoka, 420-8660, Japan
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St. John's Medical college and Hospital
Bangalore, Karnataka, 560034, India
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Szpital Uniwersytecki, Oddzial Kliniczny Hematologii
Krakow, Lesser Poland Voivodeship, 30-688, Poland
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The Alfred
Melbourne, Victoria, 3004, Australia
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Trakya Üniversitesi Tıp Fakültesi Hastanesi-Hematoloji
Edirne, 22030, Turkey (Türkiye)
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ULS São João, E.P.E.
Porto, 4200-319, Portugal
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UMHAT Sveta Marina EAD, Clinic of Pediatric Clinical Hematology and Oncology
Varna, 9010, Bulgaria
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UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology
Sofia, 1527, Bulgaria
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University Clinical Center of Republic Srpska (205)
Banja Luka, 78000, Bosnia and Herzegovina
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University Clinical Centre Kragujevac
Kragujevac, 34000, Serbia
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University of Iowa_Iowa City
Iowa City, Iowa, 52242, United States
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University of Texas San Antonio
San Antonio, Texas, 78229, United States
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Universität des Saarlandes - Hämostaseologie und Transfusionsmedizin
Homburg, 66424, Germany
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Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie
Bonn, 53127, Germany
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Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie
Zurich, 8091, Switzerland
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Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa
Lublin, 20-093, Poland
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Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu
Wroclaw, 50-367, Poland
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Uniwersytecki Szpital Kliniczny W Poznaniu
Poznan, Greater Poland Voivodeship, 60-569, Poland
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Uniwersytecki Szpital Kliniczny nr 1 Klinika Hematoonkologii i Transplantacji Szpiku
Lublin, 20-081, Poland
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Vanderbilt University Medical Center_Nashville_0
Nashville, Tennessee, 37212, United States
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Versiti, CCBD
Milwaukee, Wisconsin, 53226, United States
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Vilnius University hospital Santaros klinikos
Vilnius, LT-08661, Lithuania
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İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
Conditions
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