Daily shot could transform life for people with haemophilia

NCT ID NCT04082429

Summary

This study is testing whether a new medicine called concizumab can safely prevent bleeding episodes in people with haemophilia A or B who do not have inhibitors. Participants will give themselves a daily injection at home and track their bleeds. The goal is to see if this daily treatment works better than only treating bleeds as they happen.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • A.O.U Città Salute Scienza Torino

    Torino, 10126, Italy

  • Acıbadem Adana Hastanesi-Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • Belfast City Hospital

    Belfast, BT9 7AB, United Kingdom

  • CHU Constantine BEN BADIS/ Hematology department

    Constantine, 25000, Algeria

  • CHU de Caen - Côte de Nacre

    Caen, 14033, France

  • CMCV

    Ranipet, Tamil Nadu, 632517, India

  • Center for Blood Disorders Augusta University

    Augusta, Georgia, 30912, United States

  • Center for Inherited Blood Disorders

    Orange, California, 92868, United States

  • Centre Hospitalier Regional Et Universitaire de Brest-Hopital de La Cavale Blanche

    Brest, 29200, France

  • Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu

    Nantes, 44093, France

  • Centre Hospitalier Universitaire de Saint Etienne-Hopital Nord

    Saint-Priest-en-Jarez, 42270, France

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Children Oncohaematology department Children's Hospital,

    Vilnius, 08406, Lithuania

  • Children Regional Clinical Hospital

    Krasnodar, 350007, Russia

  • Children's Hospital Los Angeles - Endocrinology

    Los Angeles, California, 90027, United States

  • Children's Hospital of Michigan

    Detroit, Michigan, 48201, United States

  • City out-patient clinic 37, City Hemophilia Centre

    Saint Petersburg, 191186, Russia

  • Clinical Centre of Serbia, Institute for Haematology

    Belgrade, 11000, Serbia

  • Clinical Centre of Vojvodina

    Novi Sad, 21000, Serbia

  • Copenhagen Center for Heamatology

    Copenhagen, 2100, Denmark

  • Daejeon Eulji Medical Center, Eulji University

    Daejeon, 35233, South Korea

  • Daejeon Eulji University Hospital

    Daejeon, 35233, South Korea

  • Dipartimento di Ematologia Univ. Firenze

    Florence, FI, 50134, Italy

  • Eastern Health Authority

    St. John's, Newfoundland and Labrador, A1B 3V6, Canada

  • Ege Üniversitesi Hastanesi- Hematoloji

    Izmir, 35100, Turkey (Türkiye)

  • Fiona Stanley Hospital - Haemophilia and Haemostasis Centre

    Murdoch, Western Australia, 6150, Australia

  • Gazi University

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Gazi Üniversitesi Hastanesi- Hematoloji

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Hacettepe University Medical Faculty

    Ankara, 06230, Turkey (Türkiye)

  • Hacettepe Üniversitesi Hastanesi- Endokrinoloji

    Ankara, 06230, Turkey (Türkiye)

  • Haematology and Blood Bank Department

    Algiers, 16000, Algeria

  • Hamltn Hth Sci/McMstr Child Hosp

    Hamilton, Ontario, L8N 3Z5, Canada

  • Hiroshima University Hospital, Hematology

    Hiroshima, 734-8551, Japan

  • Hiroshima University Hospital_Hematology

    Hiroshima, 734-8551, Japan

  • Hopital de Bicetre

    Le Kremlin-Bicêtre, 94270, France

  • Hospital Ampang

    Ampang, Selangor, 68000, Malaysia

  • Hospital Ampang

    Ampang, Selangor, 68000, Malaysia

  • Hospital Regional Universitario de Málaga

    Málaga, 29010, Spain

  • Hospital Univ. Central de Asturias

    Oviedo, 33011, Spain

  • Hospital Universitario Dr. José Eleuterio González

    Monterrey, Nuevo León, 64460, Mexico

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Universitario y Politécnico La Fe

    Valencia, 46026, Spain

  • Hospital Virgen del Rocío

    Seville, 41013, Spain

  • Hyogo prefectural kobe children's hospital

    Hyōgo, 654-0047, Japan

  • Hyogo prefectural kobe children's hospital Dept. of Haem and Onclogy

    Hyōgo, 654-0047, Japan

  • Hôpital Pontchaillou

    Rennes, 35033, France

  • Indiana Hemophilia-Thromb Ctr

    Indianapolis, Indiana, 46260, United States

  • Institute for Mother and Child Health Care of Serbia

    Belgrade, 11070, Serbia

  • Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery

    Lviv, 79044, Ukraine

  • Instytut Hematologii i Transfuzjologii

    Warsaw, Masovian Voivodeship, 02-776, Poland

  • Istituto di Medicina Int. A. Bianchi Bonomi Univ. Milano

    Milan, MI, 20124, Italy

  • Itoigawa sogo Hospital_Department of Pediatrics

    Niigata, 941-8502, Japan

  • J K Lon Hospital

    Jaipur, Rajasthan, 302004, India

  • Jeju National University Hospital

    Jeju City, 63241, South Korea

  • Jeju National University Hospital

    Jeju-do, 63241, South Korea

  • KBC Zagreb_Hematology

    Zagreb, 10 000, Croatia

  • Koagulationsmottagning - SUS

    Malmo, 214 28, Sweden

  • Koagulationsmottagningen

    Solna, 171 64, Sweden

  • M.S. Hershey Medical Center

    Hershey, Pennsylvania, 17033, United States

  • MH Eü. Központ -Orszagos Haemophilia Kozpont

    Budapest, H-1134, Hungary

  • Michigan State University

    Lansing, Michigan, 48911, United States

  • Morozovskaya municipal children hospital

    Moscow, 119049, Russia

  • Nagoya University Hospital_Blood Transfusion

    Aichi, 466-8560, Japan

  • National Center for Child Health and Development_Hematology

    Tokyo, 157-8535, Japan

  • National Medical Research institution of haemotology

    Moscow, 125167, Russia

  • National specialized children's hospital 'OHMATDYT' - Haemostasis centre

    Kyiv, 01135, Ukraine

  • Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz

    Bratislava, 851 07, Slovakia

  • North Estonia Medical Centre Foundation

    Tallinn, 13419, Estonia

  • Novant Hlth Vasc Ins Charlotte

    Charlotte, North Carolina, 28204, United States

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Ondokuz Mayıs Üniversitesi Hastanesi - Hematoloji

    Samsun, 55139, Turkey (Türkiye)

  • Osaka National Hospital_Dept. of Infectious diseases

    Osaka, 546-0006, Japan

  • Pietersburg Hospital

    Polokwane, Limpopo, 0699, South Africa

  • Policlinico Umberto I Sezione Ematologia

    Roma, 00161, Italy

  • Ramathibodi Hospital_Department of Haematology

    Bangkok, 10400, Thailand

  • Republican Hospital n.a. V. A. Baranov

    Petrozavodsk, 185019, Russia

  • Royal Children's Hospital

    Parkville, Victoria, 3052, Australia

  • Royal Free Haemophilia Comprehensive Care Center

    London, NW3 2QG, United Kingdom

  • Royal Free Hospital - Haemophilia

    London, NW3 2QG, United Kingdom

  • Royal Hallamshire Hospital

    Sheffield, S10 2JF, United Kingdom

  • Sahyadri Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Sahyadri Super Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Saitama Children's Med Centre_Hematology-Oncology

    Saitama, 330-8777, Japan

  • Saitama Medical Univ. Hospital

    Saitama, 350-0495, Japan

  • Saitama Medical Univ. Hospital_Dep of Int Med, Cent for Hemo

    Saitama, 350-0495, Japan

  • Severance Hospital, Yonsei University Health System

    Seoul, 03722, South Korea

  • Sheba MC The Israeli National Hemophilia Center

    Tel Litwinsky, 52621, Israel

  • Shizuoka Children's Hospital

    Shizuoka, 420-8660, Japan

  • Shizuoka Children's Hospital, Hematology-Oncology

    Shizuoka, 420-8660, Japan

  • St. John's Medical college and Hospital

    Bangalore, Karnataka, 560034, India

  • Szpital Uniwersytecki, Oddzial Kliniczny Hematologii

    Krakow, Lesser Poland Voivodeship, 30-688, Poland

  • The Alfred

    Melbourne, Victoria, 3004, Australia

  • Trakya Üniversitesi Tıp Fakültesi Hastanesi-Hematoloji

    Edirne, 22030, Turkey (Türkiye)

  • ULS São João, E.P.E.

    Porto, 4200-319, Portugal

  • UMHAT Sveta Marina EAD, Clinic of Pediatric Clinical Hematology and Oncology

    Varna, 9010, Bulgaria

  • UMHAT Tsaritsa Yoanna - ISUL EAD, Pediatric clinical hematology and oncology

    Sofia, 1527, Bulgaria

  • University Clinical Center of Republic Srpska (205)

    Banja Luka, 78000, Bosnia and Herzegovina

  • University Clinical Centre Kragujevac

    Kragujevac, 34000, Serbia

  • University of Iowa_Iowa City

    Iowa City, Iowa, 52242, United States

  • University of Texas San Antonio

    San Antonio, Texas, 78229, United States

  • Universität des Saarlandes - Hämostaseologie und Transfusionsmedizin

    Homburg, 66424, Germany

  • Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie

    Bonn, 53127, Germany

  • Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie

    Zurich, 8091, Switzerland

  • Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa

    Lublin, 20-093, Poland

  • Uniwersytecki Szpital Kliniczny Im. Jana Mikulicza-Radeckiego We Wroclawiu

    Wroclaw, 50-367, Poland

  • Uniwersytecki Szpital Kliniczny W Poznaniu

    Poznan, Greater Poland Voivodeship, 60-569, Poland

  • Uniwersytecki Szpital Kliniczny nr 1 Klinika Hematoonkologii i Transplantacji Szpiku

    Lublin, 20-081, Poland

  • Vanderbilt University Medical Center_Nashville_0

    Nashville, Tennessee, 37212, United States

  • Versiti, CCBD

    Milwaukee, Wisconsin, 53226, United States

  • Vilnius University hospital Santaros klinikos

    Vilnius, LT-08661, Lithuania

  • İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.