Pompe disease brain changes under the microscope in new Long-Term study
NCT ID NCT04639336
First seen Mar 18, 2026 · Last updated Apr 29, 2026 · Updated 4 times
Summary
This study aims to learn more about how Pompe disease affects the brain and nerves over time. Researchers will use brain scans and tests of thinking, language, and movement to track changes in 45 children and adults. Participants will be followed for 3 to 6 years to better understand long-term health effects.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Duke University Medical Center
RECRUITINGDurham, North Carolina, 27710, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Conditions
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