New study aims to measure how CLN2 affects Kids' brains and bodies

NCT ID NCT03862274

ENROLLING_BY_INVITATION Knowledge-focused Sponsor: Jessica Scherr Source: ClinicalTrials.gov ↗

First seen Oct 31, 2025 · Last updated May 06, 2026 · Updated 22 times

Summary

This study follows 30 children with CLN2 Batten disease to understand how their thinking, language, and motor skills change over time. Researchers will compare children who receive treatment (cerliponase alfa) with those who do not. The goal is to improve standard care and better measure the disease's impact on development.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

Conditions

Explore the condition pages connected to this study.