New study aims to measure how CLN2 affects Kids' skills over time

NCT ID NCT03862274

ENROLLING_BY_INVITATION Knowledge-focused Sponsor: Jessica Scherr Source: ClinicalTrials.gov ↗

First seen Oct 31, 2025 · Last updated May 13, 2026 · Updated 24 times

Summary

This study follows 30 children with CLN2 Batten disease to measure changes in thinking, movement, and language skills over time. Researchers will compare children who receive the treatment cerliponase alfa with those who do not. The goal is to find better ways to track the disease and improve standard care.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

Conditions

Explore the condition pages connected to this study.