Childhood leukaemia trial seeks best chemo cocktail

NCT ID NCT02724163

First seen Jun 29, 2026 · Last updated Jun 30, 2026 · Updated 1 time

Summary

This trial investigates the best way to treat children with acute myeloid leukaemia (AML) by comparing different chemotherapy drugs and doses. It tests whether adding up to three doses of the targeted drug gemtuzumab ozogamicin to standard chemo is safe and effective. The study also compares two types of chemotherapy for induction and two different conditioning regimens for stem cell transplants. Around 700 children under 18 with AML or related conditions are taking part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Gemtuzumab ozogamicin (Mylotarg), liposomal daunorubicin, mitoxantrone, cytarabine, fludarabine, busulfan, cyclophosphamide

What this could lead to

If successful, this could identify safer, more effective chemotherapy and antibody-drug combinations for children with AML, potentially improving survival and reducing side effects.

What could go wrong

This is a large phase 3 trial, but some drug combinations were dropped early due to manufacturing issues. Results may not apply to all AML subtypes, and side effects from intensive chemo remain significant.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute myeloblastic leukemia with maturation acute myeloid leukemia myelodysplastic syndrome myeloid sarcoma Neoplasm, Residual

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Aberdeen Royal Infirmary, NHS Grampian

    Aberdeen, AB25 2ZN, United Kingdom

  • Addenbrookes Hospital, Cambridge University Hospitals NHS Foundation Trust

    Cambridge, CB2 0QQ, United Kingdom

  • Alder Hey Children's NHS Foundation Trust

    Liverpool, L12 2AP, United Kingdom

  • Birmingham Children's Hospital NHS Foundation Trust

    Birmingham, B4 6NH, United Kingdom

  • Cardiff and Vale University Health Board, Noah's Ark Children's Hospital for Wales

    Cardiff, CF14 4XW, United Kingdom

  • Centre Hospitalier Regional Universitaire Besancon - Hopital Jean Minjoz

    Besançon, France

  • Centre Hospitalier Regional Universitaire Brest - Hopital Morvan

    Brest, France

  • Centre Hospitalier Regional Universitaire De Tours - Hopital Clocheville

    Tours, France

  • Centre Hospitalier Regional Universitaire Montpellier - Hopital Arnaud-de-villeneuve

    Montpellier, France

  • Centre Hospitalier Universitaire Amiens - Picardie

    Amiens, France

  • Centre Hospitalier Universitaire D'angers

    Angers, France

  • Centre Hospitalier Universitaire De Bordeaux - Hopital Pellegrin

    Bordeaux, France

  • Centre Hospitalier Universitaire De Caen

    Caen, France

  • Centre Hospitalier Universitaire De Clermont-ferrand

    Clermont-Ferrand, France

  • Centre Hospitalier Universitaire De Grenoble

    Grenoble, France

  • Centre Hospitalier Universitaire De Limoges

    Limoges, France

  • Centre Hospitalier Universitaire De NICE

    Nice, France

  • Centre Hospitalier Universitaire De Nancy

    Nancy, France

  • Centre Hospitalier Universitaire De Nantes

    Nantes, France

  • Centre Hospitalier Universitaire De Poitiers

    Poitiers, France

  • Centre Hospitalier Universitaire De Rennes - Hopital Sud

    Rennes, France

  • Centre Hospitalier Universitaire De Rouen

    Rouen, France

  • Centre Hospitalier Universitaire De Toulouse - Hopital Des Enfants

    Toulouse, France

  • Centre Hospitalier Universitaire Dijon Bourgogne - Hopital D'enfants

    Dijon, France

  • Centre Hospitalier Universitaire Saint-etienne

    Saint-Etienne, France

  • Centre Hospitalier Universitaire Vaudois Chuv Lausanne

    Lausanne, Switzerland

  • Centre Leon Berard

    Lyon, France

  • Christchurch Hospital

    Christchurch, New Zealand

  • Chu De Reims

    Reims, France

  • Great Ormond Street Hospital For Children NHS Trust

    London, WC1N 3JH, United Kingdom

  • Hopital Armand Trousseau

    Paris, France

  • Hopital De La Timone

    Marseille, France

  • Hopital Jeanne Dr Flandre

    Lille, France

  • Hopital Robert Debre

    Paris, France

  • Hopital Saint Louis

    Paris, France

  • Hug Hopitaux Universitaires De Geneve

    Geneva, Switzerland

  • Inselspital Bern

    Bern, Switzerland

  • John Hunter Children's Hopsital

    New Lambton Heights, Australia

  • John Radcliffe Hospital, Oxford Radcliffe Hospitals NHS Trust

    Oxford, OX3 9DU, United Kingdom

  • Kantonsspital Aarau

    Aarau, Switzerland

  • Leeds General Infirmary, Leeds Teaching Hospitals NHS Trust

    Leeds, LS9 7TF, United Kingdom

  • Luzerner Kantonspital - Kinderspital Luzern

    Lucerne, Switzerland

  • Monash Children's Hospital

    Melbourne, Australia

  • NHS Greater Glasgow and Clyde, The Royal Hospital for Children

    Glasgow, G51 4TF, United Kingdom

  • NHS Lothian, Royal Hospital for Sick Children

    Edinburgh, EH9 1LF, United Kingdom

  • Nottingham University Hospitals NHS Trust

    Nottingham, NG7 2UH, United Kingdom

  • Ospedale San Giovanni

    Bellinzona, Switzerland

  • Ostschweizer Kinderspital

    Sankt Gallen, Switzerland

  • Our Lady's Hospital for Sick Children

    Dublin, Ireland

  • Perth Children's Hospital

    Perth, Australia

  • Queensland Children's Hospital

    Brisbane, Australia

  • Royal Aberdeen Children's Hospital

    Aberdeen, AB25 2ZG, United Kingdom

  • Royal Belfast Hospital for Sick Children

    Belfast, County Antrim, BT12 6BE, United Kingdom

  • Royal Childrens Hospital

    Melbourne, Australia

  • Royal Manchester Childrens' Hospital , Central Manchester University Hospitals NHS Foundation Trust

    Manchester, M13 9WL, United Kingdom

  • Sheffield Children's NHS Foundation Trust

    Sheffield, S10 2TH, United Kingdom

  • Southampton University Hospitals NHS Trust

    Southampton, SO16 6YD, United Kingdom

  • Starship Childrens Hospital

    Auckland, New Zealand

  • Strasbourg Hautepierre

    Strasbourg, France

  • Sydney Children's Hospital

    Sydney, Australia

  • The Childrens Hospital At Westmead

    Westmead, Australia

  • The Newcastle Upon Tyne Hospitals NHS Foundation Trust

    Newcastle, NE7 7DN, United Kingdom

  • The Royal Marsden NHS Foundation Trust

    London, SW3 6JJ, United Kingdom

  • University Children's Hospital Zurich

    Zurich, Switzerland

  • University College London Hospitals NHS Foundation Trust

    London, NW1 2PG, United Kingdom

  • University Hospitals Bristol NHS Foundation Trust

    Bristol, BS1 3NU, United Kingdom

  • Universitäts-Kinderspital beider

    Basel, Switzerland

  • Women and Children's Hospital Adelaide

    Adelaide, Australia