Global effort launches to map rare genetic disorder affecting children

NCT ID NCT04486768

Summary

This study is creating a global registry to track up to 500 people with CDKL5 Deficiency Disorder (CDD), a rare genetic condition. The goal is to collect information from patients and their doctors over several years to better understand the disease's symptoms, progression, and how different treatments work. No medical procedures are involved; it's purely an information-gathering effort to help guide future research and connect families with clinical trials.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for CDKL5 DEFICIENCY DISORDER (CDD) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • University of Pennsylvania Orphan Disease Center

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.