One-Shot cell therapy aims to reset immune system in devastating muscle diseases
NCT ID NCT06154252
Summary
This study is testing a one-time cell therapy called CABA-201 for adults and children with rare autoimmune diseases that cause severe muscle weakness and inflammation. The goal is to see if this treatment can safely reduce disease activity and improve muscle strength, potentially allowing patients to stop other medications. Researchers will give a single dose of the therapy, made from the patient's own modified immune cells, to about 74 participants.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Locations
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Ann & Robert H. Lurie Children's Hospital of Chicago - Accepting Young Adult and Juvenile Patients
RECRUITINGChicago, Illinois, 60611, United States
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Boston Children's Hospital - Accepting Young Adults and Juvenile Patients
RECRUITINGBoston, Massachusetts, 02115, United States
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Children's Healthcare of Atlanta - Accepting Juvenile Patients
RECRUITINGAtlanta, Georgia, 30029, United States
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Children's Hospital Colorado - Accepting Juvenile Patients
RECRUITINGAurora, Colorado, 80046, United States
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Children's Hospital at Montefiore - Accepting Young Adult and Juvenile Patients
RECRUITINGThe Bronx, New York, 10467, United States
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Children's Hospital of Philadelphia - Accepting Young Adult and Juvenile Patients
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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Duke University Medical Center - Accepting Young Adults and Juvenile Patients
RECRUITINGDurham, North Carolina, 27710, United States
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Emory University - Accepting Adult Patients
RECRUITINGAtlanta, Georgia, 30032, United States
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Hospital for Special Surgery - Accepting Adult and Juvenile Patients
RECRUITINGNew York, New York, 10021, United States
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Houston Methodist Hospital - Accepting Adult Patients
RECRUITINGHouston, Texas, 77030, United States
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Johns Hopkins All Children's Hospital - Accepting Juvenile Patients
RECRUITINGSt. Petersburg, Florida, 33701, United States
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Kings College Hospital NHS Foundation Trust - Accepting Adult Patients
RECRUITINGLondon, SE5 9RS, United Kingdom
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Manchester Royal Infirmary - Accepting Adult Patients
RECRUITINGManchester, M13 9WL, United Kingdom
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Mayo Clinic - Accepting Adult Patients
RECRUITINGRochester, Minnesota, 55902, United States
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Mayo Clinic Florida - Accepting Adult Patients
RECRUITINGJacksonville, Florida, 32224, United States
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Memorial Sloan Kettering Cancer Center - Accepting Adult and Juvenile Patients
RECRUITINGNew York, New York, 10021, United States
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National Institutes of Health - Accepting Adult and Juvenile Patients
NOT_YET_RECRUITINGBethesda, Maryland, 20892, United States
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Northwestern Memorial Hospital - Accepting Adult Patients
RECRUITINGChicago, Illinois, 60611, United States
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Oregon Health & Science University - Accepting Adult Patients
RECRUITINGPortland, Oregon, 97239, United States
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Salford Royal Hospital - Accepting Adult Patients
RECRUITINGSalford, M6 8HD, United Kingdom
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Seattle Children's Research Institute - Accepting Juvenile Patients
RECRUITINGSeattle, Washington, 98105, United States
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The University of Chicago Medical Center - Accepting Adult and Juvenile Patients
RECRUITINGChicago, Illinois, 60637, United States
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University College London Hospitals NHS Foundation Trust - Accepting Adult Patients
RECRUITINGLondon, WC1N 3BG, United Kingdom
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University of California Irvine - Accepting Adult Patients
RECRUITINGOrange, California, 92868, United States
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University of California, San Francisco Benioff Children's Hospital - Accepting Young Adult and Juvenile Patients
RECRUITINGSan Francisco, California, 94158, United States
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University of Kansas Medical Center - Accepting Adult Patients
RECRUITINGKansas City, Kansas, 66160, United States
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University of Michigan - Accepting Young Adult and Juvenile Patients
RECRUITINGAnn Arbor, Michigan, 48105, United States
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University of North Carolina at Chapel Hill - Accepting Adult Patients
NOT_YET_RECRUITINGChapel Hill, North Carolina, 27599, United States
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University of Texas MD Anderson Cancer Center - Accepting Adult Patients
RECRUITINGHouston, Texas, 77030, United States
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University of Texas Southwestern Medical Center - Accepting Juvenile Patients
RECRUITINGDallas, Texas, 75390, United States
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Vanderbilt University Medical Center - Accepting Adult Patients
RECRUITINGNashville, Tennessee, 37232, United States
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Conditions
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