One-Shot cell therapy aims to reset immune system in debilitating muscle disease

NCT ID NCT06359041

First seen Nov 01, 2025 · Last updated Apr 20, 2026 · Updated 20 times

Summary

This early-stage study is testing a single dose of an investigational cell therapy called CABA-201 for adults with generalized myasthenia gravis (gMG), a rare autoimmune disease that causes severe muscle weakness. The therapy involves collecting a patient's own immune cells, modifying them to target the B cells believed to drive the disease, and reinfusing them after a short course of chemotherapy. The main goals are to see if the treatment is safe and if it can reduce disease symptoms and autoantibodies.

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Contacts and locations

Locations

  • Baylor College of Medicine Neurology Department

    Houston, Texas, 77030, United States

  • Beth Israel Deaconess Medical Center

    Boston, Massachusetts, 02215, United States

  • Columbia University

    New York, New York, 10032, United States

  • Houston Methodist Hospital

    Houston, Texas, 77030, United States

  • Mayo Clinic - Rochester

    Rochester, Minnesota, 55905, United States

  • Mayo Clinic Florida

    Jacksonville, Florida, 32224, United States

  • Northwestern Memorial Hospital

    Chicago, Illinois, 60611, United States

  • Oregon Health & Science University

    Portland, Oregon, 97239, United States

  • Swedish Neuroscience Research

    Seattle, Washington, 98122, United States

  • UC Davis, Department of Neurology

    Sacramento, California, 95817, United States

  • University of California Irvine

    Orange, California, 92868, United States

  • University of California, San Francisco

    San Francisco, California, 94143, United States

  • University of Colorado

    Aurora, Colorado, 80045, United States

  • University of Kansas Medical Center

    Kansas City, Kansas, 66160, United States

  • University of Massachusetts Chan Medical School

    Worcester, Massachusetts, 01655, United States

  • University of Rochester Medical Center

    Rochester, New York, 14642, United States

  • University of Texas MD Anderson Cancer Center

    Houston, Texas, 77030, United States

Conditions

Explore the condition pages connected to this study.