Two-Drug combo takes on painful NF1 tumors in early trial

NCT ID NCT06502171

First seen Nov 01, 2025 · Last updated May 11, 2026 · Updated 27 times

Summary

This study tests whether combining two drugs, cabozantinib and selumetinib, can safely shrink plexiform neurofibromas in adults and teens (16+) with neurofibromatosis type 1. About 30 participants will receive the drugs in escalating doses to find the best balance of safety and effectiveness. The goal is to reduce tumor size by at least 20% within a year.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • University of Alabama at Birmingham

    Birmingham, Alabama, 34294, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

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