Scientists map Pompe's hidden toll on brain and nerves

NCT ID NCT04639336

Summary

This study aims to understand the long-term effects of Pompe disease on the brain and nervous system. Researchers will observe 45 children with Pompe disease for 3 to 6 years, using brain scans and developmental tests. The goal is to learn how the disease progresses and affects thinking, speech, and movement over time.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Duke University Medical Center

    RECRUITING

    Durham, North Carolina, 27710, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.