New drug shows promise for fragile x teens in landmark trial
NCT ID NCT05163808
First seen Feb 04, 2026 · Last updated May 15, 2026 · Updated 17 times
Summary
This study tested an experimental drug called BPN14770 in 163 teenage boys with Fragile X syndrome. The goal was to see if the drug could improve thinking skills and daily life abilities compared to a placebo. The trial had two parts: first to check how the drug moves through the body, then a blinded comparison of the drug versus placebo over 13 weeks.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Amnova Clinical Research
Irvine, California, 92604, United States
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Cincinatti Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Clinic for Special Children
Strasburg, Pennsylvania, 17579, United States
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Emory University School of Medicine
Atlanta, Georgia, 30322, United States
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Greenwood Genetic Center
Greenville, South Carolina, 29605, United States
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Icahn School of Medicine at Mount Sinai Hospital
New York, New York, 10029, United States
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Kennedy Krieger Institute
Baltimore, Maryland, 21205, United States
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Rush University Medical Center
Chicago, Illinois, 60612, United States
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Suburban Research Associates
Media, Pennsylvania, 19063, United States
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Thompson Autism & Neurodevelopment Center - CHOC
Orange, California, 92868, United States
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U Mass
Worcester, Massachusetts, 01655, United States
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UC Davis
Sacramento, California, 95817, United States
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University of Kansas Medical Center
Kansas City, Kansas, 66160, United States
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University of Miami
Miami, Florida, 33136, United States
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University of Utah and Primary Childrens Hospital
Salt Lake City, Utah, 84113, United States
Conditions
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