Gene therapy patients monitored for Long-Term safety and effectiveness
NCT ID NCT06479616
First seen Oct 31, 2025 · Last updated Apr 09, 2026 · Updated 22 times
Summary
This study follows patients with beta-thalassemia who previously received an experimental gene therapy called CS-101. Researchers will monitor these 5 participants for 2 years to check for long-term safety and see if the treatment continues to work. The study tracks whether patients remain free from blood transfusions and monitors for any delayed side effects.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Children's Hospital of Fudan University
RECRUITINGShanghai, Shanghai Municipality, 201102, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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