Gene therapy patients monitored for Long-Term safety and effectiveness

NCT ID NCT06479616

First seen Oct 31, 2025 · Last updated Apr 09, 2026 · Updated 22 times

Summary

This study follows patients with beta-thalassemia who previously received an experimental gene therapy called CS-101. Researchers will monitor these 5 participants for 2 years to check for long-term safety and see if the treatment continues to work. The study tracks whether patients remain free from blood transfusions and monitors for any delayed side effects.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Hospital of Fudan University

    RECRUITING

    Shanghai, Shanghai Municipality, 201102, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

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