Hope for youngest HAE patients: daily pill aims to stop dangerous swelling

NCT ID NCT05453968

Summary

This study is testing a daily oral medication called berotralstat to prevent painful and dangerous swelling attacks in children aged 2 to 12 with hereditary angioedema (HAE). Researchers are finding the right dose based on a child's weight and checking how safe the drug is for young patients. The goal is to give children a long-term treatment option to control their condition and reduce the number of attacks they experience.

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Contacts and locations

Locations

  • Investigative Site #1

    Vienna, Ontario, Austria

  • Investigative Site #1

    Ottawa, Ontario, Canada

  • Investigative Site #1

    Paris, France

  • Investigative Site #1

    Berlin, Germany

  • Investigative Site #1

    Tel Aviv, Israel

  • Investigative Site #1

    Padua, Italy

  • Investigative Site #1

    Krakow, Poland

  • Investigative Site #1

    Sângeorgiu de Mureş, Romania

  • Investigative Site #1

    Madrid, Spain

  • Investigative Site #1

    Bristol, United Kingdom

  • Investigative Site #2

    Marseille, France

  • Investigative Site #2

    Frankfurt, Germany

  • Investigative Site #2

    Haifa, Israel

  • Investigative Site #2

    Málaga, Spain

  • Investigative Site #3

    Grenoble, France

Conditions

Explore the condition pages connected to this study.