New hope for rare tumors? drug axitinib tested in small trial

NCT ID NCT03839498

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This phase II trial tests the drug axitinib in 6 adults with metastatic or inoperable pheochromocytoma or paraganglioma, rare tumors of the adrenal glands or nerve tissue. Axitinib works by blocking blood vessel growth that feeds tumors. The main goal is to see how many patients' tumors shrink or stop growing. Researchers will also track how long the disease stays under control and study genetic factors that might affect response.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Axitinib (a drug that blocks blood vessel growth to tumors)

What this could lead to

If it works, this could point toward a new treatment option for people with rare adrenal or nerve tumors that have spread.

What could go wrong

This is a very small, early-phase study with only 6 participants, so results may not apply widely. The drug may not shrink tumors or could cause side effects like high blood pressure or fatigue.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

paraganglioma pheochromocytoma pheochromocytoma-paraganglioma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Columbia University Irving Medical Center

    New York, New York, 10031, United States