New drug cocktail takes on deadly brain cancer

NCT ID NCT06630260

First seen Jan 22, 2026 · Last updated Jun 23, 2026 · Updated 26 times

Summary

This trial is testing two experimental drugs, avutometinib and defactinib, given together or with a standard chemotherapy (temozolomide) for people with high-grade brain tumours like glioblastoma. The study has two phases: first, to check safety and find the right dose, and second, to see if the drugs shrink tumours or delay progression. About 182 participants will be enrolled, focusing on those with specific genetic markers.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Cambridge University Hospitals

    RECRUITING

    Cambridge, CB2 0QQ, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Royal Marsden Hospital - Drug Development Unit

    RECRUITING

    Sutton, SM2 5PT, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Royal Marsden Hospital - Neuro-Oncology Unit

    RECRUITING

    Sutton, SM2 5PT, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

avutometinib and defactinib, with or without temozolomide

What this could lead to

If successful, this could point toward a new treatment option for aggressive brain tumours like glioblastoma, potentially slowing tumour growth or improving survival.

What could go wrong

This is an early phase 1/2 trial with a small number of participants, so the drugs may not prove effective or safe enough to move forward. Side effects from the combination therapy are unknown.

Conditions

The condition(s) this trial relates to.

glioblastoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.