New drug trial aims to ease debilitating muscle stiffness
NCT ID NCT06300307
Summary
This early-stage trial is testing a new drug called ATX-01 in adults with myotonic dystrophy type 1 (DM1), a genetic disorder that causes progressive muscle weakness and stiffness. The main goal is to see if the drug is safe and well-tolerated when given as a single dose or as three doses. Researchers will also check if it helps improve symptoms like hand stiffness and leg strength, which could help with daily activities.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Centre Intégré Universitaire de Santé et Services Sociaux du Saguenay-Lac-St-Jean
RECRUITINGChicoutimi, Quebec, G7H 5H6, Canada
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Fondazione Policlinico A. Gemelli- IRCCS
RECRUITINGRome, 00168, Italy
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Hospital Universitario Donostia
RECRUITINGDonostia / San Sebastian, 20014, Spain
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Institute of Myology
RECRUITINGParis, 75651, France
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Radboudumc
RECRUITINGNijmegen, 6525, Netherlands
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St. George's University Hospital
RECRUITINGLondon, SW17 0RE, United Kingdom
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The NeMO Clinical Center in Milan, Neurorehabilitation Unit, University of Milan
RECRUITINGMilan, 20162, Italy
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UCLA
RECRUITINGLos Angeles, California, 90095, United States
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University of Florida
RECRUITINGGainesville, Florida, 32610, United States
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University of Iowa Health Care - Department of Neurology
RECRUITINGIowa City, Iowa, 52242, United States
Contact
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University of Kansas Medical Center, Department of Neurology
RECRUITINGFairway, Kansas, 66205, United States
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Virginia Commonwealth University
RECRUITINGRichmond, Virginia, 23298, United States
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Contact
Conditions
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