New drug ATX-01 targets muscle stiffness in rare disease
Disease control
Recruiting now
This early-stage trial tests a new drug, ATX-01, in 56 adults aged 18 to 64 with myotonic dystrophy type 1 (DM1), a condition causing muscle stiffness and weakness. The main goal is to see if ATX-01 is safe and tolerable compared to a placebo. Participants will receive either one…
Phase: PHASE1, PHASE2 • Sponsor: ARTHEx Biotech S.L. • Aim: Disease control
Last updated May 14, 2026 12:04 UTC