New hope for kids with rare hormone disorder: drug may cut steroid doses

NCT ID NCT07159841

First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 27 times

Summary

This study tests a new medicine called atumelnant in children aged 1 to 18 with classic congenital adrenal hyperplasia, a genetic condition that disrupts hormone balance. The goal is to see if the drug can safely control hormone levels and reduce the need for daily steroid medications. About 153 participants will take part in this phase 2/3 trial, which also includes a long-term follow-up period.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • AOU Federico II

    RECRUITING

    Naples, Campania, 80131, Italy

  • APHM -Hopital La Timone Enfants

    RECRUITING

    Marseille, 13385 Cedex 5, France

  • Azienda Ospedaliera Universitaria Meyer IRCCS

    RECRUITING

    Florence, Tuscany, 50139, Italy

  • CEDIE "Centro de Investigaciones Endocrinológicas", CONICET-FEI División de Endocrinología, Hosp de Niños Ricardo Gutiérrez

    RECRUITING

    Buenos Aires, C1425EFD, Argentina

  • Centre Hospitalier Universitaire (CHU) d'Angers

    RECRUITING

    Angers, 49100, France

  • Charité - Universitätsmedizin Berlin Campus Virchow-Klinikum Klinik für pädiatrische Endokrinologie und Diabetologie

    RECRUITING

    Berlin, 13353, Germany

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Cook Children's Health Care System

    RECRUITING

    Fort Worth, Texas, 76104, United States

  • Hopital Jeanne de Flandre - CHU de Lille

    RECRUITING

    Lille, 59037, France

  • Hopital Kremlin-Bicétre - APHP Paris Saclay

    RECRUITING

    Le Kremlin-Bicêtre, 94270, France

  • Hopital Necker - Enfants Malades

    RECRUITING

    Paris, 75015, France

  • Hopital Robert Debre

    RECRUITING

    Paris, 75019, France

  • Hospital Italiano de Buenos Aires

    RECRUITING

    Buenos Aires, C1199ABB, Argentina

  • Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo (HCFMUSP)

    RECRUITING

    São Paulo, São Paulo, 05403-000, Brazil

  • Hospital de Niños de la Santísima Trinidad

    RECRUITING

    Córdoba, Córdoba Province, X5000, Argentina

  • IRCCS Istituto Giannina Gaslini

    RECRUITING

    Genoa, Liguria, 16147, Italy

  • IRCCS Ospedale San Raffaele

    RECRUITING

    Milan, Lombardy, 20132, Italy

  • Institute of Endocrinology of Diabetes, The Children's Hospital at Westmead

    NOT_YET_RECRUITING

    Westmead, New South Wales, 2145, Australia

  • Instituto Médico Especializado (IME)

    RECRUITING

    Buenos Aires, C1405BCH, Argentina

  • Instituto de Investigaciones Metabólicas

    RECRUITING

    Buenos Aires, Buenos Aires, C1012AAR, Argentina

  • Monash Children's Hospital, Monash Health

    RECRUITING

    Clayton, Victoria, 3168, Australia

  • Queensland Children's Hospital

    NOT_YET_RECRUITING

    South Brisbane, Queensland, 4101, Australia

  • Rutgers Robert Wood Johnson Medical School

    RECRUITING

    New Brunswick, New Jersey, 08901, United States

  • Sheffield Children's Hospital NHS Trust, Sheffield Children's Hospital, Western Bank

    RECRUITING

    Sheffield, S10 2TH, United Kingdom

  • UZ Gent (University Hospital Ghent)

    RECRUITING

    Ghent, East Flanders, 9000, Belgium

  • UZ Leuven (Universitair Ziekenhuis Leuven)

    RECRUITING

    Leuven, Flemish Brabant, 3000, Belgium

  • UZA (Antwerp University Hospital)

    RECRUITING

    Edegem, Antwerp, 2650, Belgium

  • University of Michigan

    RECRUITING

    Ann Arbor, Michigan, 48109, United States

  • University of Minnesota

    RECRUITING

    Minneapolis, Minnesota, 55454, United States

  • University of Virginia Health System

    RECRUITING

    Charlottesville, Virginia, 22903, United States

  • Uniwersytecki Szpital Kliniczny Nr 1 im. Prof. Tadeusza Sokotowskiego PUM w Szczecinie, Centrum Wsparcia Badan Klinicznych Pomorskiego Uniwersytetu Medycznego w Szczecinie

    RECRUITING

    Szczecin, West Pomeranian Voivodeship, 71-252, Poland

  • lnstytut Centrum Zdrowia Matki Polki, Klinika Endokrynologii i Chor6b Metabolicznych

    RECRUITING

    Lodz, Poland, 93-338, Poland

Conditions

Explore the condition pages connected to this study.