Massive global study tracks rare disease patients for better understanding

NCT ID NCT04561518

Recruiting now Knowledge-focused Sponsor: Alnylam Pharmaceuticals Source: ClinicalTrials.gov ↗

Summary

This study aims to understand how ATTR amyloidosis affects people in real-world settings, not in controlled clinical trials. Researchers will follow 1,500 patients, including those with symptoms and those carrying the gene but without symptoms, to track disease progression and how approved treatments work in everyday practice. The goal is to gather information that helps doctors better manage this rare condition.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Study contacts

Contact

Phone: •••-•••-•••• Email: •••••@•••••
Contact

Phone: •••-•••-•••• Email: •••••@•••••

Locations

Clinical Trial Site
RECRUITING

La Jolla, California, 92037, United States
Clinical Trial Site
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Los Angeles, California, 90095, United States
Clinical Trial Site
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Jacksonville, Florida, 32224, United States
Clinical Trial Site
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Iowa City, Iowa, 52242, United States
Clinical Trial Site
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Kansas City, Kansas, 66160, United States
Clinical Trial Site
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Baltimore, Maryland, 21224, United States
Clinical Trial Site
COMPLETED

Boston, Massachusetts, 02127, United States
Clinical Trial Site
RECRUITING

New York, New York, 10034, United States
Clinical Trial Site
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Durham, North Carolina, 27710, United States
Clinical Trial Site
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Columbus, Ohio, 43210, United States
Clinical Trial Site
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Philadelphia, Pennsylvania, 19104, United States
Clinical Trial Site
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Austin, Texas, 78756, United States
Clinical Trial Site
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Houston, Texas, 77030, United States
Clinical Trial Site
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Salvador, Brazil
Clinical Trial Site
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São Paulo, Brazil
Clinical Trial Site
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Sofia, Bulgaria
Clinical Trial Site
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Aarhus, Denmark
Clinical Trial Site
COMPLETED

Copenhagen, Denmark
Clinical Trial Site
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Bordeaux, France
Clinical Trial Site
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Bron, France
Clinical Trial Site
RECRUITING

Créteil, France
Clinical Trial Site
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Le Kremlin-Bicêtre, France
Clinical Trial Site
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Marseille, France
Clinical Trial Site
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Berlin, Germany
Clinical Trial Site
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Giessen, Germany
Clinical Trial Site
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Hanover, Germany
Clinical Trial Site
RECRUITING

Jerusalem, Israel
Clinical Trial Site
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Ramat Gan, Israel
Clinical Trial Site
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Milan, Italy
Clinical Trial Site
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Naples, Italy
Clinical Trial Site
RECRUITING

Palermo, Italy
Clinical Trial Site
RECRUITING

Roma, Italy
Clinical Trial Site
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Groningen, Netherlands
Clinical Trial Site
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Lisbon, Portugal
Clinical Trial Site
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Porto, Portugal
Clinical Trial Site
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Barcelona, Spain
Clinical Trial Site
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Madrid, Spain
Clinical Trial Site
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Palma, Spain
Clinical Trial Site
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New Taipei City, Taiwan
Clinical Trial Site
RECRUITING

Taipei, Taiwan

Conditions

Explore the condition pages connected to this study.

ATTR AMYLOIDOSIS TRANSTHYRETIN-MEDIATED AMYLOIDOSIS