New drug cocktail targets Hard-to-Treat brain tumors

NCT ID NCT03922555

First seen Jun 24, 2026 · Last updated Jul 24, 2026 · Updated 2 times

Summary

This early-stage trial is testing a drug called ASTX727 in adults with a type of brain tumor (glioma) that has an IDH mutation and has come back or is growing. The drug combines two substances to try to stop cancer cells from growing. The main goal is to find the highest safe dose, with 18 participants enrolled.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
ASTX727 (cedazuridine and decitabine)
What this could lead to
If it works, this could point toward a new treatment option for people with recurrent IDH-mutant gliomas, potentially slowing tumor growth.
What could go wrong
This is a very early Phase 1 trial with only 18 participants, focused on finding a safe dose. It is not yet known if ASTX727 will effectively control the cancer, and side effects are possible.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Brigham and Women's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

  • Dana Farber Cancer Institute

    RECRUITING

    Boston, Massachusetts, 02115, United States

  • Massachusetts General Hospital Cancer Center

    RECRUITING

    Boston, Massachusetts, 02114, United States