First human test of Single-Shot gene therapy for ALS begins

NCT ID NCT07287397

Summary

This is an early-stage study to check the safety of a new, one-time gene therapy called VTx-002 for people with ALS. It will involve 12 participants who will receive a single injection and be closely monitored for up to 5 years. The main goal is to see if the treatment is safe and well-tolerated, while also looking for early signs that it might slow the progression of the disease.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for AMYOTROPHIC LATERAL SCLEROSIS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Herbert Irving Comprehensive Cancer Center

    NOT_YET_RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Kings College Hospital

    NOT_YET_RECRUITING

    London, SE5 9RS, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic in Florida

    NOT_YET_RECRUITING

    Jacksonville, Florida, 32224, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Royal Hallamshire Hospital

    NOT_YET_RECRUITING

    Sheffield, S10 2JF, United Kingdom

    Contact Phone: •••-•••-••••

  • Sean M. Healey & AMG Center for ALS at Massachusetts General Hospital

    RECRUITING

    Boston, Massachusetts, 02114, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • St Joseph's Hospital and medical Center - Barrow Neurological Institute

    NOT_YET_RECRUITING

    Phoenix, Arizona, 85013, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • UMC Utrecht

    NOT_YET_RECRUITING

    Utrecht, Netherlands

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • UZ Leuven

    NOT_YET_RECRUITING

    Leuven, Belgium

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of California San Diego Medical Center

    NOT_YET_RECRUITING

    San Diego, California, 92121, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Miami School of Science

    NOT_YET_RECRUITING

    Miami, Florida, 33136, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Pennsylvania

    NOT_YET_RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.