Scientists watch rare eye disease progress to prepare for future treatments

NCT ID NCT01736293

First seen Nov 01, 2025 · Last updated Jun 09, 2026 · Updated 33 times

Summary

This study follows 68 people with ABCA4 gene mutations (linked to Stargardt disease and other retinal degenerations) for up to 10 years. Researchers collect blood and skin samples and perform detailed eye exams to track how the disease changes over time. No treatment is given; the goal is to build a group of well-studied participants ready for future clinical trials.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • National Institutes of Health Clinical Center

    Bethesda, Maryland, 20892, United States

Conditions

Explore the condition pages connected to this study.