Experimental gene injection aims to save sight in rare eye disease
Disease control
Completed
This early-stage trial tested a gene therapy called ZM-01 in just 2 boys aged 3 to 18 with X-linked retinoschisis, a rare genetic eye condition that causes vision loss. The treatment was injected into one eye to check safety and see if it improves vision. The main goal was to mon…
Phase: EARLY_PHASE1 • Sponsor: Zhongmou Therapeutics • Aim: Disease control
Last updated Jun 23, 2026 11:57 UTC