Ucb Biosciences, Inc.

This study continues testing an experimental combination therapy (doxecitine and doxribtimine) in people with thymidine kinase 2 deficiency, a rare genetic disorder that causes muscle weakness and breathing problems. The research aims to see if long-term treatment is safe and whe…

This study is testing the safety and effects of a medication called fenfluramine in very young children (1 to under 2 years old) who have Dravet syndrome, a severe form of epilepsy. The main goal is to see if the drug is safe for their hearts and bodies, while also checking if it…