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The First Affiliated Hospital Of Bengbu Medical University

Clinical trials sponsored by The First Affiliated Hospital Of Bengbu Medical University, explained in plain language.

Trials to join now! 1 Not yet recruiting 1 Not yet finished but already full! 1

One-Shot gene therapy trial offers hope for lifelong PKU management

Disease control Recruiting now

This early-stage study is testing a single intravenous infusion of an experimental gene therapy called NGGT002 in adults with phenylketonuria (PKU). The main goals are to see if the treatment is safe and if it can lower the high levels of phenylalanine (Phe) in the blood, which i…

Phase: EARLY_PHASE1 • Sponsor: The First Affiliated Hospital of Bengbu Medical University • Aim: Disease control

Last updated Mar 27, 2026 12:37 UTC