Gene therapy breakthrough targets inherited heart disease
Disease control
Recruiting now
This study tests a new gene therapy called TN-201 for people with a genetic form of hypertrophic cardiomyopathy (HCM), a condition where the heart muscle thickens and makes it harder to pump blood. The therapy uses a harmless virus to deliver a working copy of the MYBPC3 gene dir…
Phase: PHASE1, PHASE2 • Sponsor: Tenaya Therapeutics • Aim: Disease control
Last updated May 14, 2026 12:02 UTC