First human test: can mRNA fix broken muscles in DMD kids?
Disease control
Recruiting now
This early study is testing whether a new treatment called SPOT-mRNA03 is safe for boys with Duchenne muscular dystrophy (DMD). The treatment delivers genetic instructions to help muscles produce a missing protein called dystrophin. Six boys aged 2-6 will receive the treatment th…
Phase: EARLY_PHASE1 • Sponsor: Shanghai Siponuoyin Biotechnology Co Ltd • Aim: Disease control
Last updated Mar 27, 2026 12:39 UTC