New drug trial aims to protect muscle in rare genetic disease
Disease control
Not yet recruiting
This study is testing whether an investigational drug called apitegromab can help preserve muscle in adults with facioscapulohumeral muscular dystrophy (FSHD), a genetic condition that causes progressive muscle weakness. About 60 participants will receive either the drug or a pla…
Phase: PHASE2 • Sponsor: Scholar Rock, Inc. • Aim: Disease control
Last updated Apr 02, 2026 02:12 UTC