New hope for duchenne: experimental drugs aim to slow muscle decline
Disease control
Completed
This study tested two experimental drugs, casimersen and golodirsen, in 228 people with Duchenne muscular dystrophy (DMD) who have specific genetic mutations. The goal was to see if these drugs could help maintain muscle function, such as walking speed and distance, compared to a…
Phase: PHASE3 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control
Last updated May 17, 2026 07:38 UTC