Scientists test One-Shot gene injection to fight rare eye disease
Disease control
Recruiting now
This early-stage study is testing the safety and initial effects of a single gene therapy injection, called RTx-021, for people with Stargardt disease, a rare genetic condition that causes vision loss. Up to 18 patients aged 16 and older will receive the injection in one eye and …
Phase: PHASE1, PHASE2 • Sponsor: Ray Therapeutics, Inc. • Aim: Disease control
Last updated Apr 02, 2026 06:56 UTC