Rare disease study: what happens when you stop the treatment?
Disease control
Completed
This study tested what happens when males with a rare genetic disorder called MCT8 deficiency stop taking their medication, tiratricol. For 30 days, some participants received a placebo (dummy pill) instead of their regular drug to see if their thyroid hormone levels would rise t…
Phase: PHASE3 • Sponsor: Rare Thyroid Therapeutics International AB • Aim: Disease control
Last updated Mar 23, 2026 15:18 UTC