Study reveals risks of stopping thyroid drug in rare genetic disorder
Disease control
Completed
This study looked at what happens when males with MCT8 deficiency (a rare genetic condition affecting thyroid hormone transport) stop taking tiratricol. Twenty participants who were stable on the drug were randomly assigned to either continue tiratricol or receive a placebo for 3…
Phase: PHASE3 • Sponsor: Rare Thyroid Therapeutics International AB • Aim: Disease control
Last updated Apr 30, 2026 15:48 UTC