Breakthrough treatment trial offers hope for children with rare neurological disorder
Disease control
Completed
This completed Phase 3 trial tested whether a medication called EryDex could help control neurological symptoms in children with ataxia telangiectasia, a rare genetic disorder that affects movement and coordination. The study involved 105 children aged 6 and older who received ei…
Phase: PHASE3 • Sponsor: Quince Therapeutics S.p.A. • Aim: Disease control
Last updated Mar 23, 2026 15:19 UTC