Experimental drug for rare epilepsy disorders fails to complete trial
Disease control
Terminated
This study tested a drug called vatiquinone in 68 people with mitochondrial disease who have hard-to-control seizures. Participants were randomly assigned to receive either the drug or a placebo for 24 weeks, with an option to continue the drug afterward. The trial was stopped ea…
Phase: PHASE2, PHASE3 • Sponsor: PTC Therapeutics • Aim: Disease control
Last updated May 01, 2026 16:00 UTC