Missing Iron-Carrying protein replaced in rare blood disorder
Cure
Ongoing
Atransferrinemia is a rare inherited condition in which the body cannot make enough transferrin, a protein that moves iron through the blood. Without it, iron builds up in organs and red blood cells cannot form properly. Researchers are testing intravenous infusions of apotransfe…
Phase 2 • Sponsor: Prothya Biosolutions • Aim: Cure
Last updated Sep 18, 2026 00:00 UTC