Orphalan
Clinical trials sponsored by Orphalan, explained in plain language.
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New Once-Daily pill tested for rare copper disease
Disease control CompletedThis study tested whether people with Wilson's Disease prefer a new once-daily medication over their current treatment that requires multiple daily doses. Ten adults who were already on stable treatment tried the new formulation for 28 days while reporting on their satisfaction a…
Phase: PHASE2 • Sponsor: Orphalan • Aim: Disease control
Last updated Feb 19, 2026 14:37 UTC
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New blood test could sharpen monitoring for rare liver disease
Knowledge-focused CompletedThis study tested a new, more precise blood test to measure 'free' copper levels in people with Wilson's Disease. It involved 50 adult patients who had extra blood drawn during their regular doctor visits over about a year. The goal was to see if this new test provides better inf…
Sponsor: Orphalan • Aim: Knowledge-focused
Last updated Mar 23, 2026 15:15 UTC