N-lorem Foundation
Clinical trials sponsored by N-lorem Foundation, explained in plain language.
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One-of-a-Kind drug created for single ALS patient
Disease control Not yet recruitingThis study is testing a custom-made drug designed for a single person with ALS caused by a specific genetic mutation. The goal is to see if the drug is safe and if it can help slow the progression of the disease over one year. The study will carefully track the participant's phys…
Phase: PHASE1, PHASE2 • Sponsor: n-Lorem Foundation • Aim: Disease control
Last updated Apr 01, 2026 14:43 UTC
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One-of-a-Kind drug created for single Patient's devastating genetic illness
Disease control Not yet recruitingThis study is creating a custom drug for one person with a rare, inherited brain disease called DRPLA. The goal is to see if this personalized treatment is safe and can help control the patient's seizures and other symptoms. Researchers will closely monitor the patient's health a…
Phase: PHASE1, PHASE2 • Sponsor: n-Lorem Foundation • Aim: Disease control
Last updated Apr 01, 2026 14:41 UTC
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One-of-a-Kind genetic treatment trial launches for single child with Ultra-Rare disease
Disease control Not yet recruitingThis study is testing a custom-made genetic medicine for a single child with Schuurs-Hoeijmakers syndrome, a rare disorder that affects development. The goal is to see if the treatment is safe and if it can help improve the child's ability to communicate and use their hands. The …
Phase: PHASE1, PHASE2 • Sponsor: n-Lorem Foundation • Aim: Disease control
Last updated Mar 20, 2026 14:48 UTC