Hope for rare brain disease: new drug trial aims to stall deadly decline
Disease control
Recruiting now
This Phase 3 study tests whether the drug leriglitazone can help adult men with cerebral adrenoleukodystrophy (cALD), a rare and serious brain disease. The main goal is to see if the drug delays death or the need for permanent breathing support compared to a placebo. About 40 men…
Phase: PHASE3 • Sponsor: Minoryx Therapeutics, S.L. • Aim: Disease control
Last updated Jun 27, 2026 07:57 UTC