New hope for kids needing transplants: gentler prep drugs tested
Disease control
Completed
This study aimed to find a safer and effective drug treatment for children needing a stem cell transplant for serious non-cancerous diseases like immune deficiencies and metabolic disorders. It directly compared two different drug combinations used to prepare a child's body to re…
Phase: PHASE2 • Sponsor: medac GmbH • Aim: Disease control
Last updated Mar 19, 2026 14:56 UTC