New drug combo may make stem cell transplants safer for kids with blood disorders
Disease control
Completed
This study tested two different drug combinations given before a stem cell transplant in 106 children with non-cancerous diseases like immune deficiencies and blood disorders. The goal was to see if one drug (treosulfan) caused fewer serious side effects or deaths than the standa…
Phase: PHASE2 • Sponsor: medac GmbH • Aim: Disease control
Last updated May 01, 2026 15:59 UTC